Advancements in CRISPR/Cas systems for disease treatment

The clustered regularly interspaced short palindromic repeats (CRISPR)-Cas (CRISPR-associated proteins) is an adaptive immune system present in most bacteria and archaea, protecting them from infection by exogenous genetic elements. Due to its simplicity, cost-effectiveness, and precise gene editing...

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Bibliographic Details
Main Authors: Yangsong Xu, Hao Le, Qinjie Wu, Ning Wang, Changyang Gong
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:Acta Pharmaceutica Sinica B
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Online Access:http://www.sciencedirect.com/science/article/pii/S2211383525003132
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