Modulator-refractory cystic fibrosis: Defining the scope and challenges of an emerging at-risk population

Cystic fibrosis (CF) causes life-shortening respiratory and systemic disease due to dysfunction of the cystic fibrosis transmembrane conductance regulator (CFTR) chloride channel. Highly effective modulator therapies (HEMT) improve the lives of many people with cystic fibrosis (PwCF) by correcting t...

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Bibliographic Details
Main Authors: Lindsay Somerville, Larry Borish, Imre Noth, Dana Albon
Format: Article
Language:English
Published: SAGE Publishing 2024-11-01
Series:Therapeutic Advances in Respiratory Disease
Online Access:https://doi.org/10.1177/17534666241297877
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