Long-term follow-up of neurocognitive function in patients with citrin deficiency and cholestasis

Background Citrin deficiency is a rare metabolic disorder prevalent in East and Southeast Asia that affects liver or neurological function throughout various life stages. While early diagnosis and dietary management can improve prognosis for infant onset disease, data on long-term neurocognitive out...

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Main Authors: Meng-Ju Melody Tsai, Jung-Chi Chang, Heng-Yu Lu, Susan Shur-Fen Gau, Yin-Hsiu Chien, Wuh-Liang Hwu, Yen-Hsuan Ni, Huey-Ling Chen, Ni-Chung Lee
Format: Article
Language:English
Published: The Korean Pediatric Society 2025-03-01
Series:Clinical and Experimental Pediatrics
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Online Access:http://e-cep.org/upload/pdf/cep-2024-01102.pdf
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