The NeuroNEXT Gene Therapy Consortium: Designing and Advising on Quality Gene Therapy Trials in Rare and Ultra-rare Neurological Disorders

The NeuroNEXT Gene Therapy Consortium: Designing and Advising on Quality Gene Therapy Trials in Rare and Ultra-rare Neurological Disorders

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Bibliographic Details
Main Authors:	David Klements, MS, Marianne Chase, Hyun Joo (Sophie) Cho, Aleksander Videnovic, Christopher Coffey, Ph.D., Dixie Ecklund, R.N., M.S.N., M.B.A., Merit Cudkowicz, M.D., M.Sc.
Format:	Article
Language:	English
Published:	Elsevier 2025-07-01
Series:	Neurotherapeutics
Online Access:	http://www.sciencedirect.com/science/article/pii/S1878747925001230
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