Cure the Incurable: Update of Treatment in Inherited Neuromuscular Disorders

Originally thought to be incurable, huge therapeutic progress has been made in recent years in the field of inherited neuromuscular disorders. Approaches aiming to rescue the underlying pathophysiology, i.e. loss-of-function or gain-of-function mutations, have been developed via end-product replacem...

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Bibliographic Details
Main Authors: Cheng-Hao Yu, Kuan-Lin Lai
Format: Article
Language:English
Published: Wolters Kluwer Medknow Publications 2024-10-01
Series:Acta Neurologica Taiwanica
Subjects:
Online Access:https://journals.lww.com/10.4103/ANT.33-4_Review
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