Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas

Immune checkpoint inhibitor-diabetes (CPI-D) is an acute and non-resolving immune-related adverse event (irAE) initiated primarily by disrupting the programmed death-1 (PD-1)/programmed death-ligand 1 (PD-L1) axis with monoclonal antibodies. A major limitation in understanding CPI-D is the lack of a...

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Main Authors: Todd M Brusko, Ana Luisa Perdigoto, Kevan C Herold, Zoe Quandt, Arabella Young, Garry Nolan, Jee Hye Kang, Mark S Anderson, Paul L Bollyky, Graham Larson Barlow, Jennifer A Smith, Irina Kusmartseva, Shen Dong, Melanie R Shapiro, Jamie L Felton, Vinh Q Nguyen, Greg Szot, Assad A Hassoun, Maki Nakayama, Stewart Cooper
Format: Article
Language:English
Published: BMJ Publishing Group 2025-08-01
Series:Journal for ImmunoTherapy of Cancer
Online Access:https://jitc.bmj.com/content/13/8/e011818.full
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author Todd M Brusko
Ana Luisa Perdigoto
Kevan C Herold
Zoe Quandt
Arabella Young
Garry Nolan
Jee Hye Kang
Mark S Anderson
Paul L Bollyky
Graham Larson Barlow
Jennifer A Smith
Irina Kusmartseva
Shen Dong
Melanie R Shapiro
Jamie L Felton
Vinh Q Nguyen
Greg Szot
Assad A Hassoun
Maki Nakayama
Stewart Cooper
author_facet Todd M Brusko
Ana Luisa Perdigoto
Kevan C Herold
Zoe Quandt
Arabella Young
Garry Nolan
Jee Hye Kang
Mark S Anderson
Paul L Bollyky
Graham Larson Barlow
Jennifer A Smith
Irina Kusmartseva
Shen Dong
Melanie R Shapiro
Jamie L Felton
Vinh Q Nguyen
Greg Szot
Assad A Hassoun
Maki Nakayama
Stewart Cooper
author_sort Todd M Brusko
collection DOAJ
description Immune checkpoint inhibitor-diabetes (CPI-D) is an acute and non-resolving immune-related adverse event (irAE) initiated primarily by disrupting the programmed death-1 (PD-1)/programmed death-ligand 1 (PD-L1) axis with monoclonal antibodies. A major limitation in understanding CPI-D is the lack of access to pancreatic tissue from patients experiencing this complication. We report a unique patient with no prior history of diabetes or autoimmune disease whose treatment with CPI for metastatic melanoma was complicated by CPI-D requiring insulin therapy. The patient then went on to develop pancreatic cancer. In the setting of the pancreatic cancer treatment, we were able to perform detailed single-cell RNA sequencing and immunophenotyping within the surgically resected pancreas. This revealed substantial lymphocytic infiltration associated with the islets, suggestive of an autoimmune rather than autoinflammatory mechanistic origin for CPI-D.
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institution Kabale University
issn 2051-1426
language English
publishDate 2025-08-01
publisher BMJ Publishing Group
record_format Article
series Journal for ImmunoTherapy of Cancer
spelling doaj-art-ac7c7def11f54dac95a3a7702d3fe0ac2025-08-20T03:41:34ZengBMJ Publishing GroupJournal for ImmunoTherapy of Cancer2051-14262025-08-0113810.1136/jitc-2025-011818Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreasTodd M Brusko0Ana Luisa Perdigoto1Kevan C Herold2Zoe Quandt3Arabella Young4Garry Nolan5Jee Hye Kang6Mark S Anderson7Paul L Bollyky8Graham Larson Barlow9Jennifer A Smith10Irina Kusmartseva11Shen Dong12Melanie R Shapiro13Jamie L Felton14Vinh Q Nguyen15Greg Szot16Assad A Hassoun17Maki Nakayama18Stewart Cooper19Department of Pediatrics, University of Florida, Gainesville, Florida, USADepartment of Internal Medicine, Yale University, New Haven, Connecticut, USADepartment of Internal Medicine, Yale University, New Haven, Connecticut, USADepartment of Medicine, University of California San Francisco, San Francisco, California, USADiabetes Center, University of California San Francisco, San Francisco, California, USADepartment of Pathology, Stanford University School of Medicine, Stanford, California, USADiabetes Center, University of California San Francisco, San Francisco, California, USADepartment of Medicine, University of California San Francisco, San Francisco, California, USADivision of Infectious Diseases and Geographic Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California, USADivision of Infectious Diseases and Geographic Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California, USADiabetes Center, University of California San Francisco, San Francisco, California, USADepartment of Pathology, Immunology and Laboratory Medicine, University of Florida Diabetes Institute, Gainesville, Florida, USADiabetes Center, University of California San Francisco, San Francisco, California, USADepartment of Pathology, Immunology and Laboratory Medicine, University of Florida Diabetes Institute, Gainesville, Florida, USADepartment of Pediatrics, Division of Pediatric Endocrinology and the Herman B. Wells Center for Pediatric Research, Indiana University School of Medicine, Indianapolis, Indiana, USADepartment of Surgery, University of California San Francisco, San Francisco, California, USADiabetes Center, University of California San Francisco, San Francisco, California, USADepartment of Surgery, California Pacific Medical Center, San Francisco, California, USADepartment of Immunology and Microbiology, University of Colorado School of Medicine, Aurora, Colorado, USALiver Center, University of California San Francisco, San Francisco, California, USAImmune checkpoint inhibitor-diabetes (CPI-D) is an acute and non-resolving immune-related adverse event (irAE) initiated primarily by disrupting the programmed death-1 (PD-1)/programmed death-ligand 1 (PD-L1) axis with monoclonal antibodies. A major limitation in understanding CPI-D is the lack of access to pancreatic tissue from patients experiencing this complication. We report a unique patient with no prior history of diabetes or autoimmune disease whose treatment with CPI for metastatic melanoma was complicated by CPI-D requiring insulin therapy. The patient then went on to develop pancreatic cancer. In the setting of the pancreatic cancer treatment, we were able to perform detailed single-cell RNA sequencing and immunophenotyping within the surgically resected pancreas. This revealed substantial lymphocytic infiltration associated with the islets, suggestive of an autoimmune rather than autoinflammatory mechanistic origin for CPI-D.https://jitc.bmj.com/content/13/8/e011818.full
spellingShingle Todd M Brusko
Ana Luisa Perdigoto
Kevan C Herold
Zoe Quandt
Arabella Young
Garry Nolan
Jee Hye Kang
Mark S Anderson
Paul L Bollyky
Graham Larson Barlow
Jennifer A Smith
Irina Kusmartseva
Shen Dong
Melanie R Shapiro
Jamie L Felton
Vinh Q Nguyen
Greg Szot
Assad A Hassoun
Maki Nakayama
Stewart Cooper
Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas
Journal for ImmunoTherapy of Cancer
title Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas
title_full Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas
title_fullStr Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas
title_full_unstemmed Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas
title_short Autoimmune origin for immune checkpoint inhibitor-diabetes revealed by deep immune phenotyping of the pancreas
title_sort autoimmune origin for immune checkpoint inhibitor diabetes revealed by deep immune phenotyping of the pancreas
url https://jitc.bmj.com/content/13/8/e011818.full
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