Unmet needs in hereditary angioedema: an international survey of physicians

Abstract Background Hereditary angioedema (HAE) is a rare and potentially life-threatening genetic disorder characterized by unpredictable attacks of angioedema. MENTALIST (UnMEt Needs in herediTAry angioedema—a gLobal physIcian perSpecTive) is the first international survey uncovering unmet needs a...

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Main Authors: Thomas Buttgereit, Felix Aulenbacher, Adil Adatia, Carolina Vera Ayala, Maryam Ali Al-Nesf, Sabine Altrichter, Mohamed Abuzakouk, Mona Al-Ahmad, Ramzy Mohammed Ali, Alejandro Berardi, Isabelle Boccon-Gibod, Laurence Bouillet, Luisa Brussino, Marko Barešić, Paula J. Busse, Stephen D. Betschel, Herberto Chong-Neto, Oscar Calderón Llosa, Timothy J. Craig, Anthony D. Dorr, Sérgio Duarte Dortas Junior, Daria Fomina, Henriette Farkas, Jie Shen Fok, Anete S. Grumach, Jens Greve, Mar Guilarte, Margarida Gonçalo, Vesna Grivcheva-Panovska, Michihiro Hide, Roman Hakl, Ankur Jindal, Constance H. Katelaris, Shailajah Kamaleswaran, Tamar Kinaciyan, Elena Latysheva, José Ignacio Larco Sousa, Ramón Lleonart Bellfill, Hassan Mobayed, Martin Metz, Iman Nasr, Natasa T. Mitrevska, Stefania Nicola, Claudio Alberto Salvador Parisi, Grzegorz Porebski, Jonny Peter, Mariana Paes Leme Ferriani, Nelson Rosario Filho, Bülent Enis Şekerel, Faradiba Sarquis Serpa, Marcin Stobiecki, Susanne Trainotti, Anna Valerieva, Chamard Wongsa, Jane C. Y. Wong, Esra Yucel, Yinglei Li, Chiara Nenci, Marcus Maurer, Markus Magerl, Philip H. Li
Format: Article
Language:English
Published: BMC 2025-07-01
Series:Orphanet Journal of Rare Diseases
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Online Access:https://doi.org/10.1186/s13023-025-03739-8
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