SMA Community Priorities for Future Drug Therapies: Cross-Sectional Survey Findings Representing 410 Adults with SMA
Abstract Introduction Despite advances in the therapeutic landscape for spinal muscular atrophy (SMA), unmet needs for those with this condition persist. This study seeks to characterize unmet needs that adults with SMA hope future therapies will address and explores associations between reported ne...
Saved in:
| Main Authors: | Ilse S. Peterson, Ramaa Chitale, Mary A. Curry, Lisa T. Belter |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Adis, Springer Healthcare
2025-05-01
|
| Series: | Neurology and Therapy |
| Subjects: | |
| Online Access: | https://doi.org/10.1007/s40120-025-00753-7 |
| Tags: |
Add Tag
No Tags, Be the first to tag this record!
|
Similar Items
-
Serial casting for contractures in SMA: consensus derived guidelines for treatment
by: Laurey Brown, et al.
Published: (2025-04-01) -
Successful pregnancy of an SMA type 3 sitter on Nusinersen therapy - a case report
by: Miriam Hiebeler, et al.
Published: (2025-01-01) -
Correction: Serial casting for contractures in SMA: consensus derived guidelines for treatment
by: Laurey Brown, et al.
Published: (2025-07-01) -
PRMT inhibitor promotes SMN2 exon 7 inclusion and synergizes with nusinersen to rescue SMA mice
by: Anna J Kordala, et al.
Published: (2023-09-01) -
Common complications in spinal muscular atrophy (SMA) type 1 after nusinersen treatment
by: Yiğithan Güzin, et al.
Published: (2024-11-01)