SMA Community Priorities for Future Drug Therapies: Cross-Sectional Survey Findings Representing 410 Adults with SMA

Abstract Introduction Despite advances in the therapeutic landscape for spinal muscular atrophy (SMA), unmet needs for those with this condition persist. This study seeks to characterize unmet needs that adults with SMA hope future therapies will address and explores associations between reported ne...

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Bibliographic Details
Main Authors: Ilse S. Peterson, Ramaa Chitale, Mary A. Curry, Lisa T. Belter
Format: Article
Language:English
Published: Adis, Springer Healthcare 2025-05-01
Series:Neurology and Therapy
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Online Access:https://doi.org/10.1007/s40120-025-00753-7
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