Identification of novel TCOF1 mutations in Treacher Collins syndrome and their functional characterization

Abstract Background Treacher Collins syndrome (TCS) is a congenital disorder primarily caused by the mutation in the Treacle Ribosome Biogenesis Factor 1 (TCOF1) gene. However, the significance of many TCOF1 mutations remains uncertain. Results We report two novel mutations identified in two TCS fam...

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Bibliographic Details
Main Authors: Ying Chen, Run Yang, Xin Chen, Tianyu Zhang, Chenlong Li, Jing Ma
Format: Article
Language:English
Published: BMC 2025-04-01
Series:Orphanet Journal of Rare Diseases
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Online Access:https://doi.org/10.1186/s13023-025-03667-7
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