Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient

Abstract Rare diseases often result in delays in diagnosis. It is important to recognize conditions that have features of both inborn errors of immunity and predispose to myeloid neoplasia. Here we report a patient with GATA2 deficiency that presented with disseminated non‐tuberculous mycobacterial...

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Main Authors: Erica‐Mari Nell, Helena Cornellissen, Katherine Hodkinson, Michael F. Urban, Fatima Cassim Bassa, Fatima Bibi Fazel, Tracey Wiggill, Semira Irusen, Zivanai C. Chapanduka
Format: Article
Language:English
Published: Wiley 2023-03-01
Series:Clinical Case Reports
Subjects:
Online Access:https://doi.org/10.1002/ccr3.7075
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author Erica‐Mari Nell
Helena Cornellissen
Katherine Hodkinson
Michael F. Urban
Fatima Cassim Bassa
Fatima Bibi Fazel
Tracey Wiggill
Semira Irusen
Zivanai C. Chapanduka
author_facet Erica‐Mari Nell
Helena Cornellissen
Katherine Hodkinson
Michael F. Urban
Fatima Cassim Bassa
Fatima Bibi Fazel
Tracey Wiggill
Semira Irusen
Zivanai C. Chapanduka
author_sort Erica‐Mari Nell
collection DOAJ
description Abstract Rare diseases often result in delays in diagnosis. It is important to recognize conditions that have features of both inborn errors of immunity and predispose to myeloid neoplasia. Here we report a patient with GATA2 deficiency that presented with disseminated non‐tuberculous mycobacterial infection and pancytopenia secondary to myelodysplastic syndrome.
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institution Kabale University
issn 2050-0904
language English
publishDate 2023-03-01
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series Clinical Case Reports
spelling doaj-art-9e6bbd8ef3bc401c930d760f53e76a8b2025-08-20T03:47:23ZengWileyClinical Case Reports2050-09042023-03-01113n/an/a10.1002/ccr3.7075Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patientErica‐Mari Nell0Helena Cornellissen1Katherine Hodkinson2Michael F. Urban3Fatima Cassim Bassa4Fatima Bibi Fazel5Tracey Wiggill6Semira Irusen7Zivanai C. Chapanduka8Division of Haematological Pathology, Faculty of Medicine and Health Sciences Stellenbosch University and National Health Laboratory Service, Tygerberg Hospital Cape Town South AfricaDivision of Haematological Pathology, Faculty of Medicine and Health Sciences Stellenbosch University and National Health Laboratory Service, Tygerberg Hospital Cape Town South AfricaDepartment of Molecular Medicine and Haematology, Faculty of Health Sciences University of the Witwatersrand and National Health Laboratory Service Johannesburg South AfricaDivision of Molecular Biology and Human Genetics, Faculty of Medicine and Health Science Stellenbosch University Stellenbosch South AfricaDivision of Clinical Haematology, Department of Internal Medicine, Faculty of Medicine and Health Sciences Stellenbosch University and Tygerberg Hospital Cape Town South AfricaDivision of Clinical Haematology, Department of Internal Medicine, Faculty of Medicine and Health Sciences Stellenbosch University and Tygerberg Hospital Cape Town South AfricaDepartment of Molecular Medicine and Haematology, Faculty of Health Sciences University of the Witwatersrand and National Health Laboratory Service Johannesburg South AfricaDivision of Clinical Haematology, Department of Internal Medicine, Faculty of Medicine and Health Sciences Stellenbosch University and Tygerberg Hospital Cape Town South AfricaDivision of Haematological Pathology, Faculty of Medicine and Health Sciences Stellenbosch University and National Health Laboratory Service, Tygerberg Hospital Cape Town South AfricaAbstract Rare diseases often result in delays in diagnosis. It is important to recognize conditions that have features of both inborn errors of immunity and predispose to myeloid neoplasia. Here we report a patient with GATA2 deficiency that presented with disseminated non‐tuberculous mycobacterial infection and pancytopenia secondary to myelodysplastic syndrome.https://doi.org/10.1002/ccr3.7075GATA2 deficiencyinborn errors of immunitylymphoedemamyelodysplastic syndromemyeloid neoplasms with germline predispositionnon‐tuberculous mycobacterium
spellingShingle Erica‐Mari Nell
Helena Cornellissen
Katherine Hodkinson
Michael F. Urban
Fatima Cassim Bassa
Fatima Bibi Fazel
Tracey Wiggill
Semira Irusen
Zivanai C. Chapanduka
Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient
Clinical Case Reports
GATA2 deficiency
inborn errors of immunity
lymphoedema
myelodysplastic syndrome
myeloid neoplasms with germline predisposition
non‐tuberculous mycobacterium
title Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient
title_full Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient
title_fullStr Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient
title_full_unstemmed Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient
title_short Infection and myelodysplasia: A case report of GATA2 deficiency in a South African patient
title_sort infection and myelodysplasia a case report of gata2 deficiency in a south african patient
topic GATA2 deficiency
inborn errors of immunity
lymphoedema
myelodysplastic syndrome
myeloid neoplasms with germline predisposition
non‐tuberculous mycobacterium
url https://doi.org/10.1002/ccr3.7075
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