Novel loop structure of human IgG1 Fc fused CD38 targeted bispecific antibodies and their anti-tumor effect in acute myeloid leukemia

Abstract Background Acute myeloid leukemia (AML) still lacks an ideal immunotherapy target. CD38 serves as a potential therapeutic target for AML. Classical bispecific antibody (BsAb) requires continuous infusion due to small molecular size and short half-life. Methods The anti-human CD38 single-cha...

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Main Authors: Shisen Wang, Manling Chen, Tong Zhou, Chengcai Guo, Zhifeng Yan, Yingxi Xu, Haiyan Xing, Kejing Tang, Zheng Tian, Qing Rao, Shaowei Qiu, Ying Wang, Runxia Gu, Min Wang, Jianxiang Wang
Format: Article
Language:English
Published: BMC 2025-07-01
Series:Journal of Translational Medicine
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Online Access:https://doi.org/10.1186/s12967-025-06827-2
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Summary:Abstract Background Acute myeloid leukemia (AML) still lacks an ideal immunotherapy target. CD38 serves as a potential therapeutic target for AML. Classical bispecific antibody (BsAb) requires continuous infusion due to small molecular size and short half-life. Methods The anti-human CD38 single-chain variable fragment (scFv) and anti-human CD3 scFv were cloned to expression plasmids. ExpiCHO-S cells were transfected, and the anti-CD38/anti-CD3 bispecific antibody (38-3-BsAbs) in CHO supernatants was efficiently purified. The anti-AML efficacy of 38-3-BsAbs was evaluated in vitro and in vivo. Results The novel loop structures of non-human IgG Fc fused and human IgG1 Fc fused anti-CD38/anti-CD3 BsAbs, 38-3-loop-BsAb and 38-3-loopFc-BsAb, were designed and produced. Both 38-3-loop-BsAb and 38-3-loopFc-BsAb showed excellent anti-AML effects at low concentrations in vitro. AML xenograft NOD-scid IL2gammanull (NSG) mouse model was adopted to evaluate therapeutic effects of 38-3-BsAb. The anti-leukemic effect of 38-3-loopFc-BsAb was superior. Conclusions We report on new structures of 38-3 bispecific antibody and demonstrate their anti-tumor effect in the treatment of AML.
ISSN:1479-5876