Expanded‐Access Use of Elamipretide Improves Quality of Life in Patients With Rare Mitochondrial Disorders Characterized by Ophthalmic Symptoms: A Case Series

ABSTRACT This case series presents the use of elamipretide in two patients with different progressive mitochondrial disorders (chronic progressive external ophthalmoplegia [CPEO] plus and neuropathy, ataxia, and retinitis pigmentosa [NARP] syndrome) characterized by ophthalmic traits. Elamipretide w...

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Bibliographic Details
Main Authors: Sharique Ansari, Mary Kay Koenig
Format: Article
Language:English
Published: Wiley 2024-12-01
Series:Clinical Case Reports
Subjects:
Online Access:https://doi.org/10.1002/ccr3.9591
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