Inherited metabolic disorders: presentation, clinical types, laboratory diagnosis and genetic markers

Abstract Inherited metabolic disorders (IMDs) are classified under rare genetic diseases almost always presenting in newborn and infants. IMDs are classified according to the clinical presentation, diagnosis and prognosis. Several factors are involved in the IMDs pathogenesis. Moreover, almost all I...

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Bibliographic Details
Main Authors: Aamir Ijaz, Seyyedha Abbas, Maria Shabbir, Yasmin Badshah, Fizzah Abid, Tayyaba Afsar, Suhail Razak
Format: Article
Language:English
Published: BMC 2025-08-01
Series:Orphanet Journal of Rare Diseases
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Online Access:https://doi.org/10.1186/s13023-025-03979-8
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