Human-based complex in vitro models: their promise and potential for rare disease therapeutics

Human-based complex in vitro models: their promise and potential for rare disease therapeutics

Rare diseases affect a small percentage of an individual country’s population; however, with over 7,000 in total, rare diseases represent a significant disease burden impacting up to 10% of the world’s population. Despite this, there are no approved treatments for almost 95% of rare diseases, and th...

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Main Authors: Surat Parvatam, Francesca Pistollato, Lindsay J. Marshall, Fabia Furtmann, Devashree Jahagirdar, Mohua Chakraborty Choudhury, Sujata Mohanty, Harshita Mittal, Saveetha Meganathan, Rakesh Mishra
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-01-01
Series:Frontiers in Cell and Developmental Biology
Subjects:
rare diseases
organoids
iPSCs
CIVM
cystic fibrosis
organ-on-chip
Online Access:https://www.frontiersin.org/articles/10.3389/fcell.2025.1526306/full
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https://www.frontiersin.org/articles/10.3389/fcell.2025.1526306/full

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