P224: Clinical outcomes for patients enrolled in the MPS VII disease monitoring program (DMP)

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Bibliographic Details
Main Authors: Barbara Burton, Raymond Wang, Roberto Giugliani, Antonio Gonzalez-Meneses, Christina Grant, Maurizio Scarpa, Monica Penon Portmann, Esmeralda Oussoren, Esmeralda Martins, Consuelo Durand, Brigitte Chabrol, Joel Hetzer, Jeanne Cohen, J. Lawrence Merritt
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425002286
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