Kidney Outcomes in Patients With Hereditary Transthyretin Amyloid Nephropathy Treated With Transthyretin Stabilizers And Gene-Silencer Therapies

Introduction: Kidney involvement is underestimated in patients with hereditary transthyretin amyloidosis (ATTRv), and few data are available about the renal outcomes of patients treated with targeted therapies. Methods: Patients with ATTRv nephropathy (ATTRv-N) from 6 French referral centers were re...

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Main Authors: Julien Dang, Justine Solignac, Sophie Ferlicot, Charlotte Mussini, Frank Bridoux, Antoine Huart, Marie Essig, Delphine Campigli, Mickaël Bobot, Laurent Daniel, Thibaud Damy, Violaine Planté-Bordeneuve, Hamza Sakhi, Céline Labeyrie, Cécile Cauquil, Andoni Echaniz-Laguna, Ilias Kounis, Anissa Moktefi, Perrine Devic, Sarah Mouawad, Albane Brodin-Sartorius, Renaud Snanoudj, Mohamad Zaidan, Noémie Jourde-Chiche, Vincent Audard
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:Kidney International Reports
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Online Access:http://www.sciencedirect.com/science/article/pii/S246802492500172X
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