Immune responses to central nervous system directed adeno-associated virus gene therapy: Does direct CNS delivery make a difference?

Adeno-associated virus (AAV) mediated gene therapy is a leading gene delivery platform with potential to transform the landscape of treatment for neurological disorders. While AAV is deemed non-immunogenic compared to other viral vectors, adverse immune reactions have been observed in the clinic, ra...

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Bibliographic Details
Main Authors: Ashley L. Harkins, Prajakta P. Ambegaokar, Allison M. Keeler
Format: Article
Language:English
Published: Elsevier 2024-07-01
Series:Neurotherapeutics
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Online Access:http://www.sciencedirect.com/science/article/pii/S1878747924001211
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