Exploring patient-reported outcomes and morbidity burden of patients with VEXAS syndrome: a scoping reviewResearch in context

Summary: Background: VEXAS (vacuoles, E1 enzyme, X-linked, auto-inflammatory, somatic) is a recently discovered syndrome of autoinflammatory origin affecting mainly older patients with a clinical picture encompassing a variety of hematological and rheumatological conditions. We aimed to gather curr...

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Bibliographic Details
Main Authors: Fabio Efficace, Daniela Krepper, Francesco Sparano, Paola Fazi, Maria Teresa Voso, Carmelo Gurnari
Format: Article
Language:English
Published: Elsevier 2025-08-01
Series:EClinicalMedicine
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Online Access:http://www.sciencedirect.com/science/article/pii/S258953702500286X
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