Pre-clinical development of an enzyme replacement therapy (CPI-601) for CLN1 Batten disease: process development, stability and uptake studies in different species

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Bibliographic Details
Main Authors: Renuka Raman, Ph.D., Ben Horst, Ph.D., Maryam Zare, Ph.D., Zahra Shajrokh, Magdalena Leszczyniecka, Ph.D., Sean Ekins, Ph.D., D.Sc
Format: Article
Language:English
Published: Elsevier 2025-07-01
Series:Neurotherapeutics
Online Access:http://www.sciencedirect.com/science/article/pii/S187874792500131X
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