Real-World Utilization Patterns, Safety, and Efficacy of Tafamidis in Patients With Hereditary Transthyretin Amyloidosis in Japan

ABSTRACT: Purpose: Patients with hereditary transthyretin (ATTRv) amyloidosis experience progressive degeneration of the somatic and peripheral nervous system that can impair ambulation, autonomy, and quality of life (QOL). Tafamidis meglumine (tafamidis) is the first pharmacotherapy approved to sl...

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Main Authors: Hiroaki Konishi, PharmD, Hajime Abe, MD, PhD, Noriko Matsumoto, Yutaka Endo, Yoshiki Sekijima, MD, PhD, Mitsuharu Ueda, MD, PhD, Yukio Ando, MD, PhD
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Current Therapeutic Research
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Online Access:http://www.sciencedirect.com/science/article/pii/S0011393X25000189
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