Combining dynamin 2 myopathy and neuropathy mutations rescues both phenotypes

Abstract Mutations within a single gene can lead to diverse human genetic diseases affecting highly specialized tissues. Notably, dominant mutations in the DNM2 gene, encoding the mechanoenzyme dynamin, lead to distinct neuromuscular disorders: centronuclear myopathy (CNM) and Charcot-Marie-Tooth ne...

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Bibliographic Details
Main Authors: Marie Goret, Evelina Edelweiss, Jérémy Jehl, David Reiss, Patricio Aguirre-Pineda, Sylvie Friant, Jocelyn Laporte
Format: Article
Language:English
Published: Nature Portfolio 2025-05-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-025-59925-6
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