P009: Index of sustained Phe response and improvements in PKU clinical outcome assessments in patients receiving pegvaliase

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Bibliographic Details
Main Authors: Drew Levy, Naomi Schwartz, David Andrae, Sarah Rose, Hafiz Oko-osi, Ogün Sazova, Kristin Lindstrom
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425008921
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