Clinicopathological-genetic features of neutral lipid storage disease with myopathy from a Chinese neuromuscular center

Abstract Background Neutral lipid storage disease with myopathy (NLSDM) is a rare genetic myopathy caused by mutations in the patatin-like phospholipase domain-containing protein (PNPLA2) gene. To date, the number of reported cases remains limited and the correlation between disease phenotypes and g...

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Bibliographic Details
Main Authors: Yi-Ning Luan, Guan-Zhong Shi, Qiu-Xiang Li, Kun Huang, Huan Yang
Format: Article
Language:English
Published: BMC 2025-07-01
Series:Orphanet Journal of Rare Diseases
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Online Access:https://doi.org/10.1186/s13023-025-03861-7
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