Clinical perspectives on myopathic complications in nephropathic cystinosis

Abstract Patients with nephropathic cystinosis are now living into their 50s and beyond thanks to advances in medical management. Due to this shift in the natural history of the disease, monitoring for and addressing extrarenal manifestations, including myopathy, has emerged as an area of increasing...

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Bibliographic Details
Main Authors: Reza Sadjadi, Cybele Ghossein, Ewa Elenberg
Format: Article
Language:English
Published: Springer 2025-07-01
Series:Journal of Rare Diseases
Subjects:
Online Access:https://doi.org/10.1007/s44162-025-00092-z
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