Efficient GBA1 editing via HDR with ssODNs by outcompeting pseudogene-mediated gene conversion upon CRISPR/Cas9 cleavage

IntroductionCRISPR/Cas9-edited induced pluripotent stem cells (iPSCs) are valuable research models for mechanistic studies. However, gene conversion between a gene-pseudogene pair that share high sequence identity and form direct repeats in proximity on the same chromosome can interfere with the pre...

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Bibliographic Details
Main Authors: Joseph S. Lagas, Monica F. Sentmanat, Xiaoxia Cui
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-04-01
Series:Frontiers in Genome Editing
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Online Access:https://www.frontiersin.org/articles/10.3389/fgeed.2025.1581743/full
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