A father’s crusade in rare disease drug development: a case study of Elpida therapeutics and Melpida

Abstract Therapeutic development for rare diseases is difficult for pharmaceutical companies due to significant scientific challenges, extensive costs, and low financial returns. It is increasingly common for caregivers and patient advocacy groups to partner with biomedical professionals to finance...

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Bibliographic Details
Main Authors: Deanna Portero, Qingyang Xu, Aaliya Hussain, Andrew W. Lo
Format: Article
Language:English
Published: BMC 2025-07-01
Series:Orphanet Journal of Rare Diseases
Online Access:https://doi.org/10.1186/s13023-025-03892-0
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