Assessment of walking in patients with Duchenne muscular dystrophy receiving ataluren in real clinical practice

Background. Duchenne muscular dystrophy (DMD) is an X-linked recessive disease caused by a variant in the DMD gene, leading to severe disability and death at a young age. Today, in some variants in the DMD gene, etiopathogenetic therapy is possible to increase the patient’s life expectancy and impro...

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Bibliographic Details
Main Authors: D. V. Aizatulina, S. S. Nikitin
Format: Article
Language:Russian
Published: ABV-press 2025-04-01
Series:Нервно-мышечные болезни
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Online Access:https://nmb.abvpress.ru/jour/article/view/648
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