Gene therapy shines light on congenital stationary night blindness for future cures

Abstract Congenital Stationary Night Blindness (CSNB) is a non-progressive hereditary eye disease that primarily affects the retinal signal processing, resulting in significantly reduced vision under low-light conditions. CSNB encompasses various subtypes, each with distinct genetic patterns and pat...

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Bibliographic Details
Main Authors: Yi Zhang, Siqi Lin, Lingqi Yu, Xiang Lin, Shuai Qu, Qingyang Ye, Mengting Yu, Wenfeng Chen, Wenjie Wu
Format: Article
Language:English
Published: BMC 2025-04-01
Series:Journal of Translational Medicine
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Online Access:https://doi.org/10.1186/s12967-025-06392-8
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