Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation

Over the past 25 years, nuclear envelope (NE) perturbations have been reported in various experimental models with mutations in the LMNA gene. Although the hypothesis that NE perturbations from LMNA mutations are a fundamental feature of striated muscle damage has garnered wide acceptance, the molec...

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Main Author: Jason C. Choi
Format: Article
Language:English
Published: Taylor & Francis Group 2025-12-01
Series:Nucleus
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Online Access:https://www.tandfonline.com/doi/10.1080/19491034.2024.2449500
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author Jason C. Choi
author_facet Jason C. Choi
author_sort Jason C. Choi
collection DOAJ
description Over the past 25 years, nuclear envelope (NE) perturbations have been reported in various experimental models with mutations in the LMNA gene. Although the hypothesis that NE perturbations from LMNA mutations are a fundamental feature of striated muscle damage has garnered wide acceptance, the molecular sequalae provoked by the NE damage and how they underlie disease pathogenesis such as cardiomyopathy (LMNA cardiomyopathy) remain poorly understood. We recently shed light on one such consequence, by employing a cardiomyocyte-specific Lmna deletion in vivo in the adult heart. We observed extensive NE perturbations prior to cardiac function deterioration with collateral damage in the perinuclear space. The Golgi is particularly affected, leading to cytoprotective stress responses that are likely disrupted by the progressive deterioration of the Golgi itself. In this review, we discuss the etiology of LMNA cardiomyopathy with perinuclear ‘organelle trauma’ as the nexus between NE damage and disease pathogenesis.
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spelling doaj-art-07df6cecc4614df4b879ee922779d6602025-08-20T02:37:07ZengTaylor & Francis GroupNucleus1949-10341949-10422025-12-0116110.1080/19491034.2024.2449500Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutationJason C. Choi0Center for Translational Medicine, Department of Medicine, Thomas Jefferson University, Philadelphia, PA, USAOver the past 25 years, nuclear envelope (NE) perturbations have been reported in various experimental models with mutations in the LMNA gene. Although the hypothesis that NE perturbations from LMNA mutations are a fundamental feature of striated muscle damage has garnered wide acceptance, the molecular sequalae provoked by the NE damage and how they underlie disease pathogenesis such as cardiomyopathy (LMNA cardiomyopathy) remain poorly understood. We recently shed light on one such consequence, by employing a cardiomyocyte-specific Lmna deletion in vivo in the adult heart. We observed extensive NE perturbations prior to cardiac function deterioration with collateral damage in the perinuclear space. The Golgi is particularly affected, leading to cytoprotective stress responses that are likely disrupted by the progressive deterioration of the Golgi itself. In this review, we discuss the etiology of LMNA cardiomyopathy with perinuclear ‘organelle trauma’ as the nexus between NE damage and disease pathogenesis.https://www.tandfonline.com/doi/10.1080/19491034.2024.2449500Autophagycardiomyocytecardiomyopathyconditional deletionGolgilamin A/C
spellingShingle Jason C. Choi
Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation
Nucleus
Autophagy
cardiomyocyte
cardiomyopathy
conditional deletion
Golgi
lamin A/C
title Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation
title_full Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation
title_fullStr Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation
title_full_unstemmed Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation
title_short Perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function LMNA mutation
title_sort perinuclear organelle trauma at the nexus of cardiomyopathy pathogenesis arising from loss of function lmna mutation
topic Autophagy
cardiomyocyte
cardiomyopathy
conditional deletion
Golgi
lamin A/C
url https://www.tandfonline.com/doi/10.1080/19491034.2024.2449500
work_keys_str_mv AT jasoncchoi perinuclearorganelletraumaatthenexusofcardiomyopathypathogenesisarisingfromlossoffunctionlmnamutation