Engineering a bacterial toxin deaminase from the DYW-family into a novel cytosine base editor for plants and mammalian cells by Dingbo Zhang, Fiona Parth, Laura Matos da Silva, Teng-Cheong Ha, Axel Schambach, Jens Boch

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Adenovirus mediated gene delivery of α-calcitonin gene-related peptide facilitates osseointegration of implant in ovariectomized rat by Yin Guozhu, Wu yihua, You Zhu, Dai li, Zhang Tianqi, Li Jia, Zhang Shizhou

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Thrombotic Microangiopathy as an Emerging Complication of Viral Vector–Based Gene Therapy by Nora Schwotzer, Carine El Sissy, Isabelle Desguerre, Véronique Frémeaux-Bacchi, Laurent Servais, Fadi Fakhouri

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Advances in AAV-mediated gene replacement therapy for pediatric monogenic neurological disorders by Livia Zhou, Yafeng Wang, Yiran Xu, Yaodong Zhang, Changlian Zhu

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Сationic liposomes as delivery systems for nucleic acids by A. A. Mikheev, E. V. Shmendel, E. S. Zhestovskaya, G. V. Nazarov, M. A. Maslov

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Lenmeldy (atidarsagene autotemcel) for individuals with early metachromatic leukodystrophy (MLD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (... by Rahaman Navaz Gangji, Qais Abu Ali, Radhika Dhamija, Andrés Morales Corado, Sandhya Kharbanda

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Gene Therapy Medicinal Products: Non-clinical Safety Studies by O. V. Astapova, A. A. Berchatova

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The Past, the Present, and the Future of Genomic Therapies in Cardiovascular Disease by Elizabeth M. McNally, Megan J. Puckelwartz, Marcelo A. Nóbrega

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Navigating Glioma Complexity: The Role of Abnormal Signaling Pathways in Shaping Future Therapies by Qiang Chen, Jin Jin, Pian Li, Xiuping Wang, Qianyan Wang

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Nanomedicine breakthroughs in cancer and neurodegenerative disease therapy by Abdul Haque, Tariq Khan, Rayees Ul Islam, Swaleha Naseem

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Therapeutics in paediatric genetic diseases: current and future landscape by Ai Ling Koh, Saumya Shekhar Jamuar

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Treating neuromuscular diseases: unveiling gene therapy breakthroughs and pioneering future applications by Yu-Fu Wu, Jun-An Chen, Yuh-Jyh Jong

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Single‐domain antibodies targeting antithrombin reduce bleeding in hemophilic mice with or without inhibitors by Elena Barbon, Gabriel Ayme, Amel Mohamadi, Jean‐François Ottavi, Charlotte Kawecki, Caterina Casari, Sebastien Verhenne, Solenne Marmier, Laetitia van Wittenberghe, Severine Charles, Fanny Collaud, Cecile V Denis, Olivier D Christophe, Federico Mingozzi, Peter J Lenting

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Efficiency of gene therapy for sensorineural hearing loss in mouse model: A meta‐analysis by Nevra Keskin Yilmaz, Dogukan Ozen, Rafael da Costa Monsanto, Emre Ocak, Artur Koerig Schuster, Tomotaka Shimura, Sebahattin Cureoglu

Subjects: “…gene therapy…”
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Brain‐Wide Neuroregenerative Gene Therapy Improves Cognition in a Mouse Model of Alzheimer's Disease by Zheng Wu, Liang Xu, Yu Xie, Abhijeet Sambangi, Shreya Swaminathan, Zifei Pei, Wenyu Ji, Zeru Li, Yaowei Guo, Zhifei Li, Gong Chen

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Innovative gene therapy strategies for tackling obesity by Motahareh Sheikh-Hosseini, Mohammad Moarefzadeh, Alyaa Abdulhussein Alsaedi, Ahmed M. Amshawee, Sahar Kareem Al-Mozani, Ahmed Yaseen Abed, Mostafa Neissi, Peyvand Parhizkar Roudsari

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Neoglycoconjugates for the delivery of nucleic acids into eucaryotic cells by M. A. Maslov, N. G. Morozova

Subjects: “…liposomes, neoglycoconjugates, nucleic acids, targeted delivery, gene therapy.…”
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Advancing cancer gene therapy: the emerging role of nanoparticle delivery systems by Maoze Wang, Huina Liu, Jinling Huang, Ting Cai, Zhi Ping Xu, Lingxiao Zhang

Subjects: “…Cancer gene therapy…”
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Local delivery of TGF-β1-mRNA decreases fibrosis in osteochondral defects by Gianluca Fontana, Brett Nemke, Yan Lu, Connie Chamberlain, Jae-Sung Lee, Joshua A. Choe, Hongli Jiao, Michael Nelson, Margot Amitrano, Wan-Ju Li, Mark Markel, William L. Murphy

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Modular transport systems based on cationic and neutral amphiphiles for gene therapy by G. A. Serebrennikova, M. A. Maslov, N. G. Morozova

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