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Golodirsen restores DMD transcript imbalance in Duchenne Muscular Dystrophy patient muscle cells
by
Rachele Rossi
,
Silvia Torelli
,
Marc Moore
,
Pierpaolo Ala
,
Jennifer Morgan
,
Jyoti Malhotra
,
Francesco Muntoni
Published 2024-11-01
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Institution
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Article
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Francesco Muntoni
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Jennifer Morgan
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Jyoti Malhotra
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Marc Moore
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Pierpaolo Ala
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Rachele Rossi
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Silvia Torelli
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