Artificial Intelligence‐Based Approaches for AAV Vector Engineering by Fangzhi Tan, Yue Dong, Jieyu Qi, Wenwu Yu, Renjie Chai

Subjects: “…AAV vector engineering…”
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AAV6 vectors provide superior gene transfer compared to AAV9 vectors following intramyocardial administration by Jianan Wang, Timo Jonker, Aina Cervera-Barea, Zhenyu Dong, Ruud N. Visser, Evelien E. Birza, Arie R. Boender, Mischa Klerk, Yuting Yang, Joyce Visser, Marlijn S. Jansen, Tom C. Grootswagers, Cindy I. Bart, Saskia C.A. de Jager, Silke Schrödel, Christian Thirion, Osne F. Kirzner, Hanno L. Tan, Antoine A.F. de Vries, Joost P.G. Sluijter, Klaus Neef, Joris R. de Groot, Vincent M. Christoffels, Gerard J.J. Boink

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Immunologic investigations into transgene directed immune-mediated myositis following delandistrogene moxeparvovec gene therapy by Rachael A. Potter, Ida H. Moeller, Sohrab Khan, Hélène Haegel, Andreas Hollenstein, Guido Steiner, Christoph Wandel, Alexander P. Murphy, Damon R. Asher, Emanuel Palatinsky, Danielle A. Griffin, Stefanie Mason, Susan T. Iannaccone, Craig M. Zaidman, Louise R. Rodino-Klapac

Subjects: “…AAV vector…”
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Evaluation of the loading capacity and patterns of packaged DNA in AAV genomes of different sizes using long-read sequencing by Mitsuki Kosaka, Ai Fujita Sajiki, Kosuke Fujita, Kazuhisa Yamada, Kenichi Kawano, Kiichi Hirazawa, Tsuyoshi Matsuno, Masahiko Takada, Nobuhiro Shimozawa, Ken-ichi Inoue, Kenya Yuki, Koji M. Nishiguchi

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A comprehensive study of AAV tropism across C57BL/6 mice, BALB/c mice, and crab-eating macaques by Kailun Fang, Xiali Yang, Yuanhua Liu, Junhui Xia, Ruoxi Wu, Fan Yang, Canbin Feng, Xinyu Liu, Linyu Shi, Guannan Geng, Hui Yang

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AAV-mediated expression of proneural factors stimulates neurogenesis from adult Müller glia in vivo by Marina Pavlou, Marlene Probst, Lew Kaplan, Elizaveta Filippova, Aric R Prieve, Fred Rieke, Thomas A Reh

Subjects: “…AAV Vectors…”
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iPSC-hepatocyte organoids as a novel platform to predict AAV gene therapy efficacy by Estelle Berreur, Giacomo Lazzaroni, Cyrill Roth, Marco Zihlmann, Martina Stirn, Ramona Matheis, Rebecca Xicluna, Ekaterina Breous-Nystrom, Adrian B. Roth

Subjects: “…AAV vectors…”
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Liver gene therapy with intein‐mediated F8 trans‐splicing corrects mouse haemophilia A by Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, Stefano Auricchio, Antonella Iuliano, Edoardo Nusco, Simone Merlin, Cristina Olgasi, Giorgia Manni, Marco Gargaro, Francesca Fallarino, Antonia Follenzi, Alberto Auricchio

Subjects: “…AAV vectors…”
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AAVR Expression is Essential for AAV Vector Transduction in Sensory Hair Cells by Fan Wu, Guisheng Chen, Rui Hu, Peiwen Liu, Jintao Lou, Wenji Zhao, Zuhong He, Suhua Sha, Yiqing Zheng

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Activated alpha 9 integrin expression enables sensory pathway reconstruction after spinal cord injury by Katerina Stepankova, Barbora Smejkalova, Lucia Machova Urdzikova, Katerina Haveliková, Fred de Winter, Stepanka Suchankova, Joost Verhaagen, Vit Herynek, Rostislav Turecek, Jessica Kwok, James Fawcett, Pavla Jendelova

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Study of the protective efficacy of CombiMab-2 against human immunodeficiency virus type 1 in mice humanised with CD4⁺ T-lymphocytes by D. S. Leontyev, F. A. Urusov, D. V. Glazkova, B. V. Belugin, O. V. Orlova, R. R. Mintaev, G. M. Tsyganova, E. V. Bogoslovskaya, G. A. Shipulin

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Probing aspects of extracellular vesicle associated AAV allows increased vector yield and insight into its transduction and immune-evasive properties by Ming Cheng, Demitri de la Cruz, Adam V. Crain, Paula Espinoza, Carrie Ng, Zachary C. Elmore, Aravind Asokan, Casey A. Maguire

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Mass photometry as a robust method for characterizing adeno-associated virus critical quality attributes in gene therapy vector by Guangyu Wang, Lei Yu, Xi Qin, Zexin Zhou, Yong Zhou, Chenggang Liang

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Sonic Hedgehog Is an Early Oligodendrocyte Marker During Remyelination by Mariagiovanna Russo, Amina Zahaf, Abdelmoumen Kassoussi, Ariane Sharif, Hélène Faure, Elisabeth Traiffort, Martial Ruat

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Current views on etiology, diagnosis, epidemiology and gene therapy of maturity onset diabetes in the young by Lilya U. Dzhemileva, Elena N. Zakharova, Anna O. Goncharenko, Maria V. Vorontsova, S. A. Rumyantsev, Natalia G. Mokrysheva, Marina Y. Loguinova, Vladimir P. Chekhonin

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