Diverse cell types establish a pathogenic immune environment in peripheral neuropathy

Abstract Neuroinflammation plays a complex and context-dependent role in many neurodegenerative diseases. We identified a key pathogenic function of macrophages in a mouse model of a rare human congenital neuropathy in which SARM1, the central executioner of axon degeneration, is activated by hypomo...

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Main Authors: Julie Choi, Amy Strickland, Hui Qi Loo, Wendy Dong, Lilianne Barbar, A. Joseph Bloom, Yo Sasaki, Sheng Chih Jin, Aaron DiAntonio, Jeffrey Milbrandt
Format: Article
Language:English
Published: BMC 2025-05-01
Series:Journal of Neuroinflammation
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Online Access:https://doi.org/10.1186/s12974-025-03459-7
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author Julie Choi
Amy Strickland
Hui Qi Loo
Wendy Dong
Lilianne Barbar
A. Joseph Bloom
Yo Sasaki
Sheng Chih Jin
Aaron DiAntonio
Jeffrey Milbrandt
author_facet Julie Choi
Amy Strickland
Hui Qi Loo
Wendy Dong
Lilianne Barbar
A. Joseph Bloom
Yo Sasaki
Sheng Chih Jin
Aaron DiAntonio
Jeffrey Milbrandt
author_sort Julie Choi
collection DOAJ
description Abstract Neuroinflammation plays a complex and context-dependent role in many neurodegenerative diseases. We identified a key pathogenic function of macrophages in a mouse model of a rare human congenital neuropathy in which SARM1, the central executioner of axon degeneration, is activated by hypomorphic mutations in the axon survival factor NMNAT2. Macrophage depletion blocked and reversed neuropathic phenotypes in this sarmopathy model, revealing SARM1-dependent neuroimmune mechanisms as key drivers of disease pathogenesis. In this study, we investigated the impact of chronic subacute SARM1 activation on the peripheral nerve milieu using single cell/nucleus RNA-sequencing (sc/snRNA-seq). Our analyses reveal an expansion of immune cells (macrophages and T lymphocytes) and repair Schwann cells, as well as significant transcriptional alterations to a wide range of nerve-resident cell types. Notably, endoneurial fibroblasts show increased expression of chemokines (Ccl9, Cxcl5) and complement components (C3, C4b, C6) in response to chronic SARM1 activation, indicating enhanced immune cell recruitment and immune response regulation by non-immune nerve-resident cells. Analysis of CD45+ immune cells in sciatic nerves revealed an expansion of an Il1b+ macrophage subpopulation with increased expression of markers associated with phagocytosis and T cell activation/proliferation. We also found a significant increase in T cells in sarmopathic nerves. Remarkably, T cell depletion rescued motor phenotypes in the sarmopathy model. These findings delineate the significant changes chronic SARM1 activation induces in peripheral nerves and highlights the potential of immunomodulatory therapies for SARM1-dependent peripheral neurodegenerative disease.
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spelling doaj-art-fe2295f2ae4e419ba485d6e79bf03bba2025-08-20T01:53:25ZengBMCJournal of Neuroinflammation1742-20942025-05-0122111910.1186/s12974-025-03459-7Diverse cell types establish a pathogenic immune environment in peripheral neuropathyJulie Choi0Amy Strickland1Hui Qi Loo2Wendy Dong3Lilianne Barbar4A. Joseph Bloom5Yo Sasaki6Sheng Chih Jin7Aaron DiAntonio8Jeffrey Milbrandt9Department of Genetics, Washington University School of MedicineDepartment of Genetics, Washington University School of MedicineDepartment of Developmental Biology, Washington University School of MedicineDepartment of Genetics, Washington University School of MedicineDepartment of Developmental Biology, Washington University School of MedicineDepartment of Genetics, Washington University School of MedicineDepartment of Genetics, Washington University School of MedicineDepartment of Genetics, Washington University School of MedicineDepartment of Developmental Biology, Washington University School of MedicineDepartment of Genetics, Washington University School of MedicineAbstract Neuroinflammation plays a complex and context-dependent role in many neurodegenerative diseases. We identified a key pathogenic function of macrophages in a mouse model of a rare human congenital neuropathy in which SARM1, the central executioner of axon degeneration, is activated by hypomorphic mutations in the axon survival factor NMNAT2. Macrophage depletion blocked and reversed neuropathic phenotypes in this sarmopathy model, revealing SARM1-dependent neuroimmune mechanisms as key drivers of disease pathogenesis. In this study, we investigated the impact of chronic subacute SARM1 activation on the peripheral nerve milieu using single cell/nucleus RNA-sequencing (sc/snRNA-seq). Our analyses reveal an expansion of immune cells (macrophages and T lymphocytes) and repair Schwann cells, as well as significant transcriptional alterations to a wide range of nerve-resident cell types. Notably, endoneurial fibroblasts show increased expression of chemokines (Ccl9, Cxcl5) and complement components (C3, C4b, C6) in response to chronic SARM1 activation, indicating enhanced immune cell recruitment and immune response regulation by non-immune nerve-resident cells. Analysis of CD45+ immune cells in sciatic nerves revealed an expansion of an Il1b+ macrophage subpopulation with increased expression of markers associated with phagocytosis and T cell activation/proliferation. We also found a significant increase in T cells in sarmopathic nerves. Remarkably, T cell depletion rescued motor phenotypes in the sarmopathy model. These findings delineate the significant changes chronic SARM1 activation induces in peripheral nerves and highlights the potential of immunomodulatory therapies for SARM1-dependent peripheral neurodegenerative disease.https://doi.org/10.1186/s12974-025-03459-7SARM1NMNAT2SarmopathyNerve-resident cellsEndoneurial fibroblastsRepair Schwann cells
spellingShingle Julie Choi
Amy Strickland
Hui Qi Loo
Wendy Dong
Lilianne Barbar
A. Joseph Bloom
Yo Sasaki
Sheng Chih Jin
Aaron DiAntonio
Jeffrey Milbrandt
Diverse cell types establish a pathogenic immune environment in peripheral neuropathy
Journal of Neuroinflammation
SARM1
NMNAT2
Sarmopathy
Nerve-resident cells
Endoneurial fibroblasts
Repair Schwann cells
title Diverse cell types establish a pathogenic immune environment in peripheral neuropathy
title_full Diverse cell types establish a pathogenic immune environment in peripheral neuropathy
title_fullStr Diverse cell types establish a pathogenic immune environment in peripheral neuropathy
title_full_unstemmed Diverse cell types establish a pathogenic immune environment in peripheral neuropathy
title_short Diverse cell types establish a pathogenic immune environment in peripheral neuropathy
title_sort diverse cell types establish a pathogenic immune environment in peripheral neuropathy
topic SARM1
NMNAT2
Sarmopathy
Nerve-resident cells
Endoneurial fibroblasts
Repair Schwann cells
url https://doi.org/10.1186/s12974-025-03459-7
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