The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease

In recent years, induced pluripotent stem cells (iPSCs) were widely used for investigating the mechanisms of Parkinson’s disease (PD). Somatic cells from patients with SNCA (α-synuclein), LRRK2 (leucine-rich repeat kinase 2), PINK1 (PTEN induced putative kinase 1), Parkin mutations, and at-risk indi...

Full description

Saved in:
Bibliographic Details
Main Authors: Ji-feng Kang, Bei-sha Tang, Ji-feng Guo
Format: Article
Language:English
Published: Wiley 2016-01-01
Series:Stem Cells International
Online Access:http://dx.doi.org/10.1155/2016/4126214
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850161927774273536
author Ji-feng Kang
Bei-sha Tang
Ji-feng Guo
author_facet Ji-feng Kang
Bei-sha Tang
Ji-feng Guo
author_sort Ji-feng Kang
collection DOAJ
description In recent years, induced pluripotent stem cells (iPSCs) were widely used for investigating the mechanisms of Parkinson’s disease (PD). Somatic cells from patients with SNCA (α-synuclein), LRRK2 (leucine-rich repeat kinase 2), PINK1 (PTEN induced putative kinase 1), Parkin mutations, and at-risk individuals carrying GBA (β-glucocerebrosidase) mutations have been successfully induced to iPSCs and subsequently differentiated into dopaminergic (DA) neurons. Importantly, some PD-related cell phenotypes, including α-synuclein aggregation, mitophagy, damaged mitochondrial DNA, and mitochondrial dysfunction, have been described in these iPSCs models, which further investigated the pathogenesis of PD. In 2007, Takahashi et al. and Vodyanik et al. generated iPSCs from human somatic cells for the first time. Since then, patients derived iPSCs were applied for disease modeling, drug discovery and screening, autologous cell replacement therapy, and other biological applications. iPSC research has now become a hot topic in a wide range of fields. This review summarizes the recent progress of PD patients derived iPSC models in pathogenic mechanism investigation and potential clinical applications, especially their promising strategy in pharmacological study and DA neurons transplantation therapy. However, the challenges of iPSC transplantation still exist, and it has a long way to go before it can be used in clinical application.
format Article
id doaj-art-fd72e0b05f1f4bcaaf37f434173930a5
institution OA Journals
issn 1687-966X
1687-9678
language English
publishDate 2016-01-01
publisher Wiley
record_format Article
series Stem Cells International
spelling doaj-art-fd72e0b05f1f4bcaaf37f434173930a52025-08-20T02:22:40ZengWileyStem Cells International1687-966X1687-96782016-01-01201610.1155/2016/41262144126214The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s DiseaseJi-feng Kang0Bei-sha Tang1Ji-feng Guo2Department of Neurology, Xiangya Hospital, Central South University, Changsha, Hunan 410008, ChinaDepartment of Neurology, Xiangya Hospital, Central South University, Changsha, Hunan 410008, ChinaDepartment of Neurology, Xiangya Hospital, Central South University, Changsha, Hunan 410008, ChinaIn recent years, induced pluripotent stem cells (iPSCs) were widely used for investigating the mechanisms of Parkinson’s disease (PD). Somatic cells from patients with SNCA (α-synuclein), LRRK2 (leucine-rich repeat kinase 2), PINK1 (PTEN induced putative kinase 1), Parkin mutations, and at-risk individuals carrying GBA (β-glucocerebrosidase) mutations have been successfully induced to iPSCs and subsequently differentiated into dopaminergic (DA) neurons. Importantly, some PD-related cell phenotypes, including α-synuclein aggregation, mitophagy, damaged mitochondrial DNA, and mitochondrial dysfunction, have been described in these iPSCs models, which further investigated the pathogenesis of PD. In 2007, Takahashi et al. and Vodyanik et al. generated iPSCs from human somatic cells for the first time. Since then, patients derived iPSCs were applied for disease modeling, drug discovery and screening, autologous cell replacement therapy, and other biological applications. iPSC research has now become a hot topic in a wide range of fields. This review summarizes the recent progress of PD patients derived iPSC models in pathogenic mechanism investigation and potential clinical applications, especially their promising strategy in pharmacological study and DA neurons transplantation therapy. However, the challenges of iPSC transplantation still exist, and it has a long way to go before it can be used in clinical application.http://dx.doi.org/10.1155/2016/4126214
spellingShingle Ji-feng Kang
Bei-sha Tang
Ji-feng Guo
The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease
Stem Cells International
title The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease
title_full The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease
title_fullStr The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease
title_full_unstemmed The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease
title_short The Progress of Induced Pluripotent Stem Cells as Models of Parkinson’s Disease
title_sort progress of induced pluripotent stem cells as models of parkinson s disease
url http://dx.doi.org/10.1155/2016/4126214
work_keys_str_mv AT jifengkang theprogressofinducedpluripotentstemcellsasmodelsofparkinsonsdisease
AT beishatang theprogressofinducedpluripotentstemcellsasmodelsofparkinsonsdisease
AT jifengguo theprogressofinducedpluripotentstemcellsasmodelsofparkinsonsdisease
AT jifengkang progressofinducedpluripotentstemcellsasmodelsofparkinsonsdisease
AT beishatang progressofinducedpluripotentstemcellsasmodelsofparkinsonsdisease
AT jifengguo progressofinducedpluripotentstemcellsasmodelsofparkinsonsdisease