Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine

Abstract The Cryptosporidium parasite is one of the leading causes of diarrheal morbidity and mortality in children, and adolescent infections are associated with chronic malnutrition. There are no vaccines available for protection and only one drug approved for treatment that has limited efficacy....

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Main Authors: Lucy C. Watson, Katarzyna A. Sala, Netanya Bernitz, Lotta Baumgärtel, Mitchell A. Pallett, N. Bishara Marzook, Lorian Cobra Straker, Duo Peng, Lucy Collinson, Adam Sateriale
Format: Article
Language:English
Published: Nature Portfolio 2025-08-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-025-63012-1
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author Lucy C. Watson
Katarzyna A. Sala
Netanya Bernitz
Lotta Baumgärtel
Mitchell A. Pallett
N. Bishara Marzook
Lorian Cobra Straker
Duo Peng
Lucy Collinson
Adam Sateriale
author_facet Lucy C. Watson
Katarzyna A. Sala
Netanya Bernitz
Lotta Baumgärtel
Mitchell A. Pallett
N. Bishara Marzook
Lorian Cobra Straker
Duo Peng
Lucy Collinson
Adam Sateriale
author_sort Lucy C. Watson
collection DOAJ
description Abstract The Cryptosporidium parasite is one of the leading causes of diarrheal morbidity and mortality in children, and adolescent infections are associated with chronic malnutrition. There are no vaccines available for protection and only one drug approved for treatment that has limited efficacy. A major barrier to developing new therapeutics is a lack of foundational knowledge of Cryptosporidium biology, including which parasite genes are essential for survival and virulence. Here, we iteratively improve the tools for genetically manipulating Cryptosporidium and develop a targeted CRISPR-based screening method to rapidly assess how the loss of individual parasite genes influence survival in vivo. Using this method, we examine the parasite’s pyrimidine salvage pathway and a set of leading Cryptosporidium vaccine candidates. From this latter group, using inducible knockout, we determined the parasite gene known as Cp23 to be essential for survival in vivo. Parasites deficient in Cp23 were able to replicate within and emerge from infected epithelial cells, yet unable to initiate gliding motility which is required for the reinfection of neighbouring cells. The targeted screening method presented here is highly versatile and will enable researchers to more rapidly expand the knowledge base for Cryptosporidium infection biology, paving the way for new therapeutics.
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institution Kabale University
issn 2041-1723
language English
publishDate 2025-08-01
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spelling doaj-art-fd6e0d4e5b3b467a8f371770160d48a62025-08-24T11:37:14ZengNature PortfolioNature Communications2041-17232025-08-0116111310.1038/s41467-025-63012-1Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestineLucy C. Watson0Katarzyna A. Sala1Netanya Bernitz2Lotta Baumgärtel3Mitchell A. Pallett4N. Bishara Marzook5Lorian Cobra Straker6Duo Peng7Lucy Collinson8Adam Sateriale9Cryptosporidiosis Laboratory, The Francis Crick InstituteCryptosporidiosis Laboratory, The Francis Crick InstituteCryptosporidiosis Laboratory, The Francis Crick InstituteCryptosporidiosis Laboratory, The Francis Crick InstituteCryptosporidiosis Laboratory, The Francis Crick InstituteCryptosporidiosis Laboratory, The Francis Crick InstituteElectron Microscopy Science Technology Platform, The Francis Crick InstituteChan Zuckerberg BiohubElectron Microscopy Science Technology Platform, The Francis Crick InstituteCryptosporidiosis Laboratory, The Francis Crick InstituteAbstract The Cryptosporidium parasite is one of the leading causes of diarrheal morbidity and mortality in children, and adolescent infections are associated with chronic malnutrition. There are no vaccines available for protection and only one drug approved for treatment that has limited efficacy. A major barrier to developing new therapeutics is a lack of foundational knowledge of Cryptosporidium biology, including which parasite genes are essential for survival and virulence. Here, we iteratively improve the tools for genetically manipulating Cryptosporidium and develop a targeted CRISPR-based screening method to rapidly assess how the loss of individual parasite genes influence survival in vivo. Using this method, we examine the parasite’s pyrimidine salvage pathway and a set of leading Cryptosporidium vaccine candidates. From this latter group, using inducible knockout, we determined the parasite gene known as Cp23 to be essential for survival in vivo. Parasites deficient in Cp23 were able to replicate within and emerge from infected epithelial cells, yet unable to initiate gliding motility which is required for the reinfection of neighbouring cells. The targeted screening method presented here is highly versatile and will enable researchers to more rapidly expand the knowledge base for Cryptosporidium infection biology, paving the way for new therapeutics.https://doi.org/10.1038/s41467-025-63012-1
spellingShingle Lucy C. Watson
Katarzyna A. Sala
Netanya Bernitz
Lotta Baumgärtel
Mitchell A. Pallett
N. Bishara Marzook
Lorian Cobra Straker
Duo Peng
Lucy Collinson
Adam Sateriale
Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine
Nature Communications
title Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine
title_full Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine
title_fullStr Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine
title_full_unstemmed Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine
title_short Targeted CRISPR screens reveal genes essential for Cryptosporidium survival in the host intestine
title_sort targeted crispr screens reveal genes essential for cryptosporidium survival in the host intestine
url https://doi.org/10.1038/s41467-025-63012-1
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