Lenmeldy (atidarsagene autotemcel) for individuals with early metachromatic leukodystrophy (MLD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)

Lenmeldy (atidarsagene autotemcel) for individuals with early metachromatic leukodystrophy (MLD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)

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Bibliographic Details
Main Authors:	Rahaman Navaz Gangji, Qais Abu Ali, Radhika Dhamija, Andrés Morales Corado, Sandhya Kharbanda
Format:	Article
Language:	English
Published:	Elsevier 2025-01-01
Series:	Genetics in Medicine Open
Subjects:	Atidarsagene autotemcel Gene therapy Lenmeldy Metachromatic leukodystrophy
Online Access:	http://www.sciencedirect.com/science/article/pii/S2949774425014712
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