Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis

Abstract: Bruton tyrosine kinase inhibitors (BTKis) have led to changes in the treatment algorithm for patients with high-risk relapsed/refractory (R/R) chronic lymphocytic leukemia (CLL), defined based on the presence of genetic mutations. Given the lack of head-to-head trials comparing next-genera...

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Main Authors: Mazyar Shadman, Jennifer R. Brown, Leyla Mohseninejad, Keri Yang, Heather Burnett, Binod Neupane, Rhys Williams, Nicole Lamanna, Susan M. O'Brien, Alessandra Tedeschi, Constantine S. Tam
Format: Article
Language:English
Published: Elsevier 2025-06-01
Series:Blood Advances
Online Access:http://www.sciencedirect.com/science/article/pii/S2473952925002162
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author Mazyar Shadman
Jennifer R. Brown
Leyla Mohseninejad
Keri Yang
Heather Burnett
Binod Neupane
Rhys Williams
Nicole Lamanna
Susan M. O'Brien
Alessandra Tedeschi
Constantine S. Tam
author_facet Mazyar Shadman
Jennifer R. Brown
Leyla Mohseninejad
Keri Yang
Heather Burnett
Binod Neupane
Rhys Williams
Nicole Lamanna
Susan M. O'Brien
Alessandra Tedeschi
Constantine S. Tam
author_sort Mazyar Shadman
collection DOAJ
description Abstract: Bruton tyrosine kinase inhibitors (BTKis) have led to changes in the treatment algorithm for patients with high-risk relapsed/refractory (R/R) chronic lymphocytic leukemia (CLL), defined based on the presence of genetic mutations. Given the lack of head-to-head trials comparing next-generation BTKis used to treat high-risk R/R disease, a network meta-analysis (NMA) was performed to estimate their relative efficacy. High-risk populations were defined based on the prespecified definitions within each trial, including patients with del(17p) and/or TP53 mutations in the ALPINE (n = 150) and ASCEND (n = 86) trials, and del(17p)/del(11q) in the ELEVATE-RR (n = 533) trial. Bayesian NMAs found zanubrutinib to be the most efficacious treatment for high-risk patients, with significantly reduced risk of progression or death compared with ibrutinib (hazard ratio [HR], 0.49; 95% credible interval [CrI], 0.31-0.78), acalabrutinib (HR, 0.55; 95% CrI, 0.32-0.94), and bendamustine + rituximab or idelalisib + rituximab (BR/IR; HR, 0.12; 95% CrI, 0.05-0.26). Differences in overall survival demonstrated a numerical trend favoring zanubrutinib (probability better than ≥80%) compared with ibrutinib (HR, 0.59; 95% CrI, 0.31-1.11), acalabrutinib (HR, 0.72; 95% CrI, 0.35-1.50), and BR/IR (HR, 0.65; 95% CrI, 0.23-1.75). Rates of response also demonstrated trends favoring zanubrutinib compared with acalabrutinib, with significant results compared with ibrutinib. The NMA suggests that the most efficacious BTKi for patients with high-risk R/R CLL is zanubrutinib.
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spelling doaj-art-ee2620bcdd8942b4b7bfa0785cf1960f2025-08-20T03:46:45ZengElsevierBlood Advances2473-95292025-06-019122863287010.1182/bloodadvances.2024014523Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysisMazyar Shadman0Jennifer R. Brown1Leyla Mohseninejad2Keri Yang3Heather Burnett4Binod Neupane5Rhys Williams6Nicole Lamanna7Susan M. O'Brien8Alessandra Tedeschi9Constantine S. Tam10Clinical Research Division, Fred Hutchinson Cancer Center and Hematology and Oncology Division, University of Washington, Seattle, WA; Correspondence: Mazyar Shadman, Fred Hutchinson Cancer Research Center, 1100 Fairview Ave N, M2-B861, Seattle, WA 98109;Chronic Lymphocytic Leukemia Center, Division of Medical Oncology, Dana-Farber Cancer Institute and Harvard Medical School, Boston, MABeOne Medicines Ltd, Schiphol, The NetherlandsBeOne Medicines Ltd, San Mateo, CAEvidera, Montreal, CanadaEvidera, Montreal, CanadaBeOne Medicines Ltd, San Mateo, CAHematology/Oncology, Herbert Irving Comprehensive Cancer Center, Columbia University Medical Center, New York, NYDivision of Hematology/Oncology, School of Medicine, University of California, Irvine, CADepartment of Hematology, Azienda Socio Sanitaria Grande Ospedale Metropolitano Niguarda, Milan, ItalyLymphoma Service, Alfred Hospital and Monash University, Melbourne, Victoria, AustraliaAbstract: Bruton tyrosine kinase inhibitors (BTKis) have led to changes in the treatment algorithm for patients with high-risk relapsed/refractory (R/R) chronic lymphocytic leukemia (CLL), defined based on the presence of genetic mutations. Given the lack of head-to-head trials comparing next-generation BTKis used to treat high-risk R/R disease, a network meta-analysis (NMA) was performed to estimate their relative efficacy. High-risk populations were defined based on the prespecified definitions within each trial, including patients with del(17p) and/or TP53 mutations in the ALPINE (n = 150) and ASCEND (n = 86) trials, and del(17p)/del(11q) in the ELEVATE-RR (n = 533) trial. Bayesian NMAs found zanubrutinib to be the most efficacious treatment for high-risk patients, with significantly reduced risk of progression or death compared with ibrutinib (hazard ratio [HR], 0.49; 95% credible interval [CrI], 0.31-0.78), acalabrutinib (HR, 0.55; 95% CrI, 0.32-0.94), and bendamustine + rituximab or idelalisib + rituximab (BR/IR; HR, 0.12; 95% CrI, 0.05-0.26). Differences in overall survival demonstrated a numerical trend favoring zanubrutinib (probability better than ≥80%) compared with ibrutinib (HR, 0.59; 95% CrI, 0.31-1.11), acalabrutinib (HR, 0.72; 95% CrI, 0.35-1.50), and BR/IR (HR, 0.65; 95% CrI, 0.23-1.75). Rates of response also demonstrated trends favoring zanubrutinib compared with acalabrutinib, with significant results compared with ibrutinib. The NMA suggests that the most efficacious BTKi for patients with high-risk R/R CLL is zanubrutinib.http://www.sciencedirect.com/science/article/pii/S2473952925002162
spellingShingle Mazyar Shadman
Jennifer R. Brown
Leyla Mohseninejad
Keri Yang
Heather Burnett
Binod Neupane
Rhys Williams
Nicole Lamanna
Susan M. O'Brien
Alessandra Tedeschi
Constantine S. Tam
Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis
Blood Advances
title Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis
title_full Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis
title_fullStr Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis
title_full_unstemmed Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis
title_short Comparative efficacy of Bruton tyrosine kinase inhibitors in high-risk relapsed/refractory CLL: a network meta-analysis
title_sort comparative efficacy of bruton tyrosine kinase inhibitors in high risk relapsed refractory cll a network meta analysis
url http://www.sciencedirect.com/science/article/pii/S2473952925002162
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