P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam*
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| Main Authors: | , , , , |
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| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2025-01-01
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| Series: | Genetics in Medicine Open |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2949774425001669 |
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| _version_ | 1849711932580298752 |
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| author | Dung Dung-Chi Khanh Nguyen Hang Nguyen Ngoc Can Dung Vu |
| author_facet | Dung Dung-Chi Khanh Nguyen Hang Nguyen Ngoc Can Dung Vu |
| author_sort | Dung Dung-Chi |
| collection | DOAJ |
| format | Article |
| id | doaj-art-ed63c3195a054b99ae06e8a4551582dc |
| institution | DOAJ |
| issn | 2949-7744 |
| language | English |
| publishDate | 2025-01-01 |
| publisher | Elsevier |
| record_format | Article |
| series | Genetics in Medicine Open |
| spelling | doaj-art-ed63c3195a054b99ae06e8a4551582dc2025-08-20T03:14:28ZengElsevierGenetics in Medicine Open2949-77442025-01-01310212710.1016/j.gimo.2025.102127P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam*Dung Dung-Chi0Khanh Nguyen1Hang Nguyen2Ngoc Can3Dung Vu4Vietnam National Children's HospitalVietnam National Children's HospitalVietnam National Children's HospitalVietnam National Children's HospitalVietnam National Children's Hospitalhttp://www.sciencedirect.com/science/article/pii/S2949774425001669 |
| spellingShingle | Dung Dung-Chi Khanh Nguyen Hang Nguyen Ngoc Can Dung Vu P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam* Genetics in Medicine Open |
| title | P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam* |
| title_full | P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam* |
| title_fullStr | P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam* |
| title_full_unstemmed | P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam* |
| title_short | P162: Registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in Vietnam* |
| title_sort | p162 registry and gene replacement therapy for spinal muscular atrophy at referral center of pediatrics in vietnam |
| url | http://www.sciencedirect.com/science/article/pii/S2949774425001669 |
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