LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment

Abstract Lipid nanoparticle (LNP)-mRNA vaccines have demonstrated protective capability in combating SARS-CoV-2. Their extensive deployment across the global population leads to the broad presence of T-cell immunity against the SARS-CoV-2 spike protein, presenting an opportunity to harness this immu...

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Main Authors: Yonger Xue, Xucheng Hou, Yichen Zhong, Yuebao Zhang, Shi Du, Diana D. Kang, Leiming Wang, Chang Wang, Haoyuan Li, Siyu Wang, Zhengwei Liu, Meng Tian, Kaiyuan Guo, Dinglingge Cao, Binbin Deng, David W. McComb, Eric Purisic, Jinye Dai, Pauline Hamon, Brian D. Brown, Nadejda M. Tsankova, Miriam Merad, Darrell J. Irvine, Ron Weiss, Yizhou Dong
Format: Article
Language:English
Published: Nature Portfolio 2025-03-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-025-57149-2
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author Yonger Xue
Xucheng Hou
Yichen Zhong
Yuebao Zhang
Shi Du
Diana D. Kang
Leiming Wang
Chang Wang
Haoyuan Li
Siyu Wang
Zhengwei Liu
Meng Tian
Kaiyuan Guo
Dinglingge Cao
Binbin Deng
David W. McComb
Eric Purisic
Jinye Dai
Pauline Hamon
Brian D. Brown
Nadejda M. Tsankova
Miriam Merad
Darrell J. Irvine
Ron Weiss
Yizhou Dong
author_facet Yonger Xue
Xucheng Hou
Yichen Zhong
Yuebao Zhang
Shi Du
Diana D. Kang
Leiming Wang
Chang Wang
Haoyuan Li
Siyu Wang
Zhengwei Liu
Meng Tian
Kaiyuan Guo
Dinglingge Cao
Binbin Deng
David W. McComb
Eric Purisic
Jinye Dai
Pauline Hamon
Brian D. Brown
Nadejda M. Tsankova
Miriam Merad
Darrell J. Irvine
Ron Weiss
Yizhou Dong
author_sort Yonger Xue
collection DOAJ
description Abstract Lipid nanoparticle (LNP)-mRNA vaccines have demonstrated protective capability in combating SARS-CoV-2. Their extensive deployment across the global population leads to the broad presence of T-cell immunity against the SARS-CoV-2 spike protein, presenting an opportunity to harness this immunological response as a universal antigen target for cancer treatment. Herein, we design and synthesize a series of amino alcohol- or amino acid-derived ionizable lipids (AA lipids) and develop an LNP-RNA-based antigen presentation platform to redirect spike-specific T-cell immunity against cancer in mouse models. First, in a prime-boost regimen, AA2 LNP encapsulating spike mRNA elicit stronger T-cell immunity against the spike epitopes compared to FDA-approved LNPs (ALC-0315 and SM-102), highlighting the superior delivery efficiency of AA2 LNP. Next, AA15V LNP efficiently delivers self-amplifying RNAs (saRNAs) encoding spike epitope-loaded single-chain trimer (sSE-SCT) MHC I molecules into tumor tissues, thereby inducing the presentation of spike epitopes. Our results show that a single intratumoral (i.t.) treatment of AA15V LNP-sSE-SCTs suppresses tumor growth and extends the survival of B16F10 melanoma and A20 lymphoma tumor-bearing mice vaccinated with AA2 LNP-spike mRNA. Additionally, AA15V LNP-sSE-SCTs enable SE-SCT expression in ex vivo human glioblastoma and lung cancer samples, suggesting its potential in clinical translation.
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spelling doaj-art-eb3d9c9048b94ce3af2377a15c82def42025-08-20T01:57:25ZengNature PortfolioNature Communications2041-17232025-03-0116111310.1038/s41467-025-57149-2LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatmentYonger Xue0Xucheng Hou1Yichen Zhong2Yuebao Zhang3Shi Du4Diana D. Kang5Leiming Wang6Chang Wang7Haoyuan Li8Siyu Wang9Zhengwei Liu10Meng Tian11Kaiyuan Guo12Dinglingge Cao13Binbin Deng14David W. McComb15Eric Purisic16Jinye Dai17Pauline Hamon18Brian D. Brown19Nadejda M. Tsankova20Miriam Merad21Darrell J. Irvine22Ron Weiss23Yizhou Dong24Division of Pharmaceutics & Pharmacology, College of Pharmacy, The Ohio State UniversityIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiDivision of Pharmaceutics & Pharmacology, College of Pharmacy, The Ohio State UniversityDivision of Pharmaceutics & Pharmacology, College of Pharmacy, The Ohio State UniversityDivision of Pharmaceutics & Pharmacology, College of Pharmacy, The Ohio State UniversityIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiDivision of Pharmaceutics & Pharmacology, College of Pharmacy, The Ohio State UniversityIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiCenter for Electron Microscopy and Analysis, The Ohio State UniversityCenter for Electron Microscopy and Analysis, The Ohio State UniversityDepartment of Pharmacological Sciences, Icahn School of Medicine at Mount SinaiDepartment of Pharmacological Sciences, Icahn School of Medicine at Mount SinaiMarc and Jennifer Lipschultz Precision Immunology Institute, Icahn School of Medicine at Mount SinaiIcahn Genomics Institute, Icahn School of Medicine at Mount SinaiFriedman Brain Institute, Icahn School of Medicine at Mount SinaiMarc and Jennifer Lipschultz Precision Immunology Institute, Icahn School of Medicine at Mount SinaiDepartment of Biological Engineering, Massachusetts Institute of TechnologyDepartment of Biological Engineering, Massachusetts Institute of TechnologyDivision of Pharmaceutics & Pharmacology, College of Pharmacy, The Ohio State UniversityAbstract Lipid nanoparticle (LNP)-mRNA vaccines have demonstrated protective capability in combating SARS-CoV-2. Their extensive deployment across the global population leads to the broad presence of T-cell immunity against the SARS-CoV-2 spike protein, presenting an opportunity to harness this immunological response as a universal antigen target for cancer treatment. Herein, we design and synthesize a series of amino alcohol- or amino acid-derived ionizable lipids (AA lipids) and develop an LNP-RNA-based antigen presentation platform to redirect spike-specific T-cell immunity against cancer in mouse models. First, in a prime-boost regimen, AA2 LNP encapsulating spike mRNA elicit stronger T-cell immunity against the spike epitopes compared to FDA-approved LNPs (ALC-0315 and SM-102), highlighting the superior delivery efficiency of AA2 LNP. Next, AA15V LNP efficiently delivers self-amplifying RNAs (saRNAs) encoding spike epitope-loaded single-chain trimer (sSE-SCT) MHC I molecules into tumor tissues, thereby inducing the presentation of spike epitopes. Our results show that a single intratumoral (i.t.) treatment of AA15V LNP-sSE-SCTs suppresses tumor growth and extends the survival of B16F10 melanoma and A20 lymphoma tumor-bearing mice vaccinated with AA2 LNP-spike mRNA. Additionally, AA15V LNP-sSE-SCTs enable SE-SCT expression in ex vivo human glioblastoma and lung cancer samples, suggesting its potential in clinical translation.https://doi.org/10.1038/s41467-025-57149-2
spellingShingle Yonger Xue
Xucheng Hou
Yichen Zhong
Yuebao Zhang
Shi Du
Diana D. Kang
Leiming Wang
Chang Wang
Haoyuan Li
Siyu Wang
Zhengwei Liu
Meng Tian
Kaiyuan Guo
Dinglingge Cao
Binbin Deng
David W. McComb
Eric Purisic
Jinye Dai
Pauline Hamon
Brian D. Brown
Nadejda M. Tsankova
Miriam Merad
Darrell J. Irvine
Ron Weiss
Yizhou Dong
LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment
Nature Communications
title LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment
title_full LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment
title_fullStr LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment
title_full_unstemmed LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment
title_short LNP-RNA-mediated antigen presentation leverages SARS-CoV-2-specific immunity for cancer treatment
title_sort lnp rna mediated antigen presentation leverages sars cov 2 specific immunity for cancer treatment
url https://doi.org/10.1038/s41467-025-57149-2
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