Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies

Congenital diaphragmatic hernia (CDH) is a complex disorder whereby improper formation of the diaphragm allows herniation of the internal organs into the thoracic cavity, resulting in pulmonary hypoplasia among other complications. Although epithelial dysfunction is central to CDH pathology, relativ...

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Main Authors: Ophelia Aubert, Olivia M. Dinwoodie, Richard Wagner, Xingbin Ai
Format: Article
Language:English
Published: MDPI AG 2025-05-01
Series:Cells
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Online Access:https://www.mdpi.com/2073-4409/14/10/687
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author Ophelia Aubert
Olivia M. Dinwoodie
Richard Wagner
Xingbin Ai
author_facet Ophelia Aubert
Olivia M. Dinwoodie
Richard Wagner
Xingbin Ai
author_sort Ophelia Aubert
collection DOAJ
description Congenital diaphragmatic hernia (CDH) is a complex disorder whereby improper formation of the diaphragm allows herniation of the internal organs into the thoracic cavity, resulting in pulmonary hypoplasia among other complications. Although epithelial dysfunction is central to CDH pathology, relatively little attention has been paid to the underlying mechanisms orchestrating epithelial malfunction. Proinflammatory signaling downstream of impaired mechanotransduction due to in utero lung compression has been elucidated to drive epithelial cell phenotypes. This has been illustrated by a reduction in nuclear YAP and the upregulation of NF-kB in CDH models. In this review, we draw from recent findings using emerging technologies to examine epithelial cell mechanisms in CDH and discuss the role of compression as a central and, crucially, sufficient driver of CDH phenotypes. In recognition of the limitations of using genetic knockout models to recapitulate such a heterogenic and etiologically complicated disease, we discuss alternative models such as the established nitrofen rat model, air–liquid interface (ALI) cultures, organoids and ex vivo lung explants. Throughout, we acknowledge the importance of involving mechanical compression in the modeling of CDH in order to faithfully recapitulate the disease. Finally, we explore novel therapeutic strategies from stem cell and regenerative therapies to precision medicine and the importance of defining CDH endotypes in order to guide treatments.
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spelling doaj-art-eb33134eb62e476ca186843636ff0ea22025-08-20T01:56:17ZengMDPI AGCells2073-44092025-05-01141068710.3390/cells14100687Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging TherapiesOphelia Aubert0Olivia M. Dinwoodie1Richard Wagner2Xingbin Ai3Department of Pediatric Surgery, University Medical Center Mannheim, 68165 Mannheim, GermanyDivision of Newborn Medicine, Department of Pediatrics, Massachusetts General Hospital, Harvard Medical School, Boston, MA 02114, USADepartment of Pediatric Surgery, University Hospital Leipzig, 04103 Leipzig, GermanyDivision of Newborn Medicine, Department of Pediatrics, Massachusetts General Hospital, Harvard Medical School, Boston, MA 02114, USACongenital diaphragmatic hernia (CDH) is a complex disorder whereby improper formation of the diaphragm allows herniation of the internal organs into the thoracic cavity, resulting in pulmonary hypoplasia among other complications. Although epithelial dysfunction is central to CDH pathology, relatively little attention has been paid to the underlying mechanisms orchestrating epithelial malfunction. Proinflammatory signaling downstream of impaired mechanotransduction due to in utero lung compression has been elucidated to drive epithelial cell phenotypes. This has been illustrated by a reduction in nuclear YAP and the upregulation of NF-kB in CDH models. In this review, we draw from recent findings using emerging technologies to examine epithelial cell mechanisms in CDH and discuss the role of compression as a central and, crucially, sufficient driver of CDH phenotypes. In recognition of the limitations of using genetic knockout models to recapitulate such a heterogenic and etiologically complicated disease, we discuss alternative models such as the established nitrofen rat model, air–liquid interface (ALI) cultures, organoids and ex vivo lung explants. Throughout, we acknowledge the importance of involving mechanical compression in the modeling of CDH in order to faithfully recapitulate the disease. Finally, we explore novel therapeutic strategies from stem cell and regenerative therapies to precision medicine and the importance of defining CDH endotypes in order to guide treatments.https://www.mdpi.com/2073-4409/14/10/687congenital diaphragmatic hernialung compressionairway epitheliummechanotransductionYAPNFkB
spellingShingle Ophelia Aubert
Olivia M. Dinwoodie
Richard Wagner
Xingbin Ai
Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies
Cells
congenital diaphragmatic hernia
lung compression
airway epithelium
mechanotransduction
YAP
NFkB
title Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies
title_full Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies
title_fullStr Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies
title_full_unstemmed Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies
title_short Epithelial Dysfunction in Congenital Diaphragmatic Hernia: Mechanisms, Models and Emerging Therapies
title_sort epithelial dysfunction in congenital diaphragmatic hernia mechanisms models and emerging therapies
topic congenital diaphragmatic hernia
lung compression
airway epithelium
mechanotransduction
YAP
NFkB
url https://www.mdpi.com/2073-4409/14/10/687
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AT oliviamdinwoodie epithelialdysfunctionincongenitaldiaphragmaticherniamechanismsmodelsandemergingtherapies
AT richardwagner epithelialdysfunctionincongenitaldiaphragmaticherniamechanismsmodelsandemergingtherapies
AT xingbinai epithelialdysfunctionincongenitaldiaphragmaticherniamechanismsmodelsandemergingtherapies