Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes

Aim. Based on strict criteria, to assess incidence, pretransplantation risk factors, and outcomes of severe hypofunction of graft, i.e. poor graft function (sPGF), following allogeneic hematopoietic stem cell transplantation (allo-HSCT) in adults. Materials & Methods. The trial included 710 adu...

Full description

Saved in:
Bibliographic Details
Main Authors: TA Rudakova, AD Kulagin, OU Klimova, IK Golubovskaya, EI Darskaya, TA Bykova, AG Smirnova, EV Morozova, SN Bondarenko, IS Moiseev, AV Beinarovich, DE Pevtsov, AL Alyanskii, EV Babenko, IM Barkhatov, BV Afanas’ev
Format: Article
Language:Russian
Published: Practical Medicine Publishing House 2019-05-01
Series:Клиническая онкогематология
Subjects:
Online Access: http://bloodjournal.ru/wp-content/uploads/2019/06/10.pdf
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850230094448033792
author TA Rudakova
AD Kulagin
OU Klimova
IK Golubovskaya
EI Darskaya
TA Bykova
AG Smirnova
EV Morozova
SN Bondarenko
IS Moiseev
AV Beinarovich
DE Pevtsov
AL Alyanskii
EV Babenko
IM Barkhatov
BV Afanas’ev
author_facet TA Rudakova
AD Kulagin
OU Klimova
IK Golubovskaya
EI Darskaya
TA Bykova
AG Smirnova
EV Morozova
SN Bondarenko
IS Moiseev
AV Beinarovich
DE Pevtsov
AL Alyanskii
EV Babenko
IM Barkhatov
BV Afanas’ev
author_sort TA Rudakova
collection DOAJ
description Aim. Based on strict criteria, to assess incidence, pretransplantation risk factors, and outcomes of severe hypofunction of graft, i.e. poor graft function (sPGF), following allogeneic hematopoietic stem cell transplantation (allo-HSCT) in adults. Materials & Methods. The trial included 710 adult patients (median age was 31 years, range 18–70 years; 55 % male and 45 % female patients) with different hematological diseases and documented transplant engraftment after allo-HSCT from matched sibling (20 %), unrelated (67 %) and haploidentical (13 %) donors in the period from 2008 to 2016. Myeloablative and reduced-intensity conditioning regimens were administered in 30 % and 70 % of patients, respectively. The analysis was based on the following sPGF criteria: 2 or more lines of cytopenia (thrombocytes < 20 × 109/L, absolute neutrophil count < 0.5 × 109/L, and hemoglobin < 70 g/L at any time after documented engraftment), complete or stable mixed donor chimerism > 90 %, and absence of relapse signs, rejection, and severe acute graft-versus-host reaction. The following factors were analyzed: age, sex, diagnosis, presence/absence of remission in acute leukemias, ferritin level, type of donor, HLA-match, blood group and sex match, transplant origin, number of transplanted CD34+ cells, and conditioning regimen. Multivariate analysis included parameters of univariate analysis with p < 0.05. Results. After allo-HSCT sPGF was identified in 103 patients with 2-year cumulative incidence of 15 % (95% confidence interval [95% CI] 12–18 %). In most cases sPGF developed during the 1st year after allo-HSCT (median 50 days). Bi- and trilineage cytopenia was found in 59 % and 41 % of cases, respectively. In multivariate analysis sPGF risk was associated with myelodysplastic syndrome, myeloproliferative disorders (hazard ratio [HR] 3.403; 95% CI 1.972–5.606; p < 0.0001), and haploidentical donors (HR 3.830; 95% CI 1.545–8.828; p = 0.001). The absence of remission at the time of allo-HSCT in acute leukemias and blood group incompatibility were of borderline significance. In 50 % of cases sPGF determined poor outcome, including death from cytopenia-related complications, further relapses, and graft rejection. Prognosis of bilineage sPGF was slightly more favorable than that of trilineage sPGF. Conclusion. The present large cohort trial yielded the incidence and analyzed the structure of sPGF in adult patients with oncohematological diseases. In addition, the key pretransplantation sPGF risk factors were identified. The results of the trial can serve to optimize the choice of therapy after allo-HSCT.
format Article
id doaj-art-e901f10c998c474daacd5dfe4bca359f
institution OA Journals
issn 1997-6933
2500-2139
language Russian
publishDate 2019-05-01
publisher Practical Medicine Publishing House
record_format Article
series Клиническая онкогематология
spelling doaj-art-e901f10c998c474daacd5dfe4bca359f2025-08-20T02:03:58ZrusPractical Medicine Publishing HouseКлиническая онкогематология1997-69332500-21392019-05-0112330831810.21320/2500-2139-2019-12-3-309-31819976933Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and OutcomesTA Rudakova0AD Kulagin1OU Klimova2IK Golubovskaya3EI Darskaya4TA Bykova5AG Smirnova6EV Morozova7SN Bondarenko8IS Moiseev9AV Beinarovich10DE Pevtsov11AL Alyanskii12EV Babenko13IM Barkhatov14BV Afanas’ev15 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 RM Gorbacheva Scientific Research Institute of Pediatric Oncology, Hematology and Transplantation; IP Pavlov First Saint Petersburg State Medical University, 6/8 L’va Tolstogo str., Saint Petersburg, Russian Federation, 197022 Aim. Based on strict criteria, to assess incidence, pretransplantation risk factors, and outcomes of severe hypofunction of graft, i.e. poor graft function (sPGF), following allogeneic hematopoietic stem cell transplantation (allo-HSCT) in adults. Materials & Methods. The trial included 710 adult patients (median age was 31 years, range 18–70 years; 55 % male and 45 % female patients) with different hematological diseases and documented transplant engraftment after allo-HSCT from matched sibling (20 %), unrelated (67 %) and haploidentical (13 %) donors in the period from 2008 to 2016. Myeloablative and reduced-intensity conditioning regimens were administered in 30 % and 70 % of patients, respectively. The analysis was based on the following sPGF criteria: 2 or more lines of cytopenia (thrombocytes < 20 × 109/L, absolute neutrophil count < 0.5 × 109/L, and hemoglobin < 70 g/L at any time after documented engraftment), complete or stable mixed donor chimerism > 90 %, and absence of relapse signs, rejection, and severe acute graft-versus-host reaction. The following factors were analyzed: age, sex, diagnosis, presence/absence of remission in acute leukemias, ferritin level, type of donor, HLA-match, blood group and sex match, transplant origin, number of transplanted CD34+ cells, and conditioning regimen. Multivariate analysis included parameters of univariate analysis with p < 0.05. Results. After allo-HSCT sPGF was identified in 103 patients with 2-year cumulative incidence of 15 % (95% confidence interval [95% CI] 12–18 %). In most cases sPGF developed during the 1st year after allo-HSCT (median 50 days). Bi- and trilineage cytopenia was found in 59 % and 41 % of cases, respectively. In multivariate analysis sPGF risk was associated with myelodysplastic syndrome, myeloproliferative disorders (hazard ratio [HR] 3.403; 95% CI 1.972–5.606; p < 0.0001), and haploidentical donors (HR 3.830; 95% CI 1.545–8.828; p = 0.001). The absence of remission at the time of allo-HSCT in acute leukemias and blood group incompatibility were of borderline significance. In 50 % of cases sPGF determined poor outcome, including death from cytopenia-related complications, further relapses, and graft rejection. Prognosis of bilineage sPGF was slightly more favorable than that of trilineage sPGF. Conclusion. The present large cohort trial yielded the incidence and analyzed the structure of sPGF in adult patients with oncohematological diseases. In addition, the key pretransplantation sPGF risk factors were identified. The results of the trial can serve to optimize the choice of therapy after allo-HSCT. http://bloodjournal.ru/wp-content/uploads/2019/06/10.pdf allogeneic hematopoietic stem cell transplantationpoor graft function
spellingShingle TA Rudakova
AD Kulagin
OU Klimova
IK Golubovskaya
EI Darskaya
TA Bykova
AG Smirnova
EV Morozova
SN Bondarenko
IS Moiseev
AV Beinarovich
DE Pevtsov
AL Alyanskii
EV Babenko
IM Barkhatov
BV Afanas’ev
Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes
Клиническая онкогематология
allogeneic hematopoietic stem cell transplantation
poor graft function
title Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes
title_full Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes
title_fullStr Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes
title_full_unstemmed Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes
title_short Severe Hypofunction of Allogeneic Hematopoietic Stem Cell Transplant in Patients with Oncohematological Diseases: Incidence, Risk Factors, and Outcomes
title_sort severe hypofunction of allogeneic hematopoietic stem cell transplant in patients with oncohematological diseases incidence risk factors and outcomes
topic allogeneic hematopoietic stem cell transplantation
poor graft function
url http://bloodjournal.ru/wp-content/uploads/2019/06/10.pdf
work_keys_str_mv AT tarudakova severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT adkulagin severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT ouklimova severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT ikgolubovskaya severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT eidarskaya severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT tabykova severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT agsmirnova severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT evmorozova severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT snbondarenko severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT ismoiseev severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT avbeinarovich severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT depevtsov severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT alalyanskii severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT evbabenko severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT imbarkhatov severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes
AT bvafanasev severehypofunctionofallogeneichematopoieticstemcelltransplantinpatientswithoncohematologicaldiseasesincidenceriskfactorsandoutcomes