Common complications in spinal muscular atrophy (SMA) type 1 after nusinersen treatment
Background. Spinal muscular atrophy (SMA) is an inherited disease with progressive muscle weakness and atrophy. Despite the new treatments developed recently, primary and secondary effects of muscle weakness in patients with SMA cause mortality and morbidity. The aim of this study is to identify co...
Saved in:
| Main Authors: | Yiğithan Güzin, Osman Büyükşen, Pınar Gençpınar, Nihal Olgaç Dündar, Figen Baydan |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Hacettepe University Institute of Child Health
2024-11-01
|
| Series: | The Turkish Journal of Pediatrics |
| Subjects: | |
| Online Access: | https://turkjpediatr.org/article/view/4527 |
| Tags: |
Add Tag
No Tags, Be the first to tag this record!
|
Similar Items
-
The efficacy and safety of nusinersen within the expanded access program in Russia
by: S. B. Artemieva, et al.
Published: (2020-12-01) -
Nusinersen corrects L-arginine deficiency in the cerebrospinal fluid of patients with severe spinal muscular atrophy
by: Amber Hassan, et al.
Published: (2025-10-01) -
Experience of Nusinersen in children with proximal spinal muscular atrophy 5q in Moscow region
by: M. V. Panteleeva
Published: (2022-12-01) -
Nusinersen for children with type I spinal muscular atrophy: 4 years’ clinical experience in Turkish cohort
by: Ömer Bektaş, et al.
Published: (2025-03-01) -
Long‐Term Effects of Nusinersen Dosing Frequency on Adult Patients With Spinal Muscular Atrophy: Efficacy of a 6‐Month Dosing Interval
by: Keita Takahashi, et al.
Published: (2025-05-01)