Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma

Abstract Central serous chorioretinopathy is an eye disease characterized by fluid buildup under the central retina whose etiology is not well understood. Abnormal choroidal veins in central serous chorioretinopathy patients have been shown to have similarities with varicose veins. To identify poten...

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Main Authors: Joel T. Rämö, Bryan R. Gorman, Lu-Chen Weng, Sean J. Jurgens, Panisa Singhanetr, Marisa G. Tieger, Elon HC van Dijk, Christopher W. Halladay, Xin Wang, Blake M. Hauser, Soo Hyun Kim, Joost Brinks, Seung Hoan Choi, Yuyang Luo, FinnGen, VA Million Veteran Program, Saiju Pyarajan, Cari L. Nealon, Michael B. Gorin, Wen-Chih Wu, Scott A. Anthony, David P. Roncone, Lucia Sobrin, Kai Kaarniranta, Suzanne Yzer, Aarno Palotie, Neal S. Peachey, Joni A. Turunen, Camiel JF Boon, Patrick T. Ellinor, Sudha K. Iyengar, Mark J. Daly, Elizabeth J. Rossin
Format: Article
Language:English
Published: Nature Portfolio 2025-05-01
Series:Nature Communications
Online Access:https://doi.org/10.1038/s41467-025-58686-6
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author Joel T. Rämö
Bryan R. Gorman
Lu-Chen Weng
Sean J. Jurgens
Panisa Singhanetr
Marisa G. Tieger
Elon HC van Dijk
Christopher W. Halladay
Xin Wang
Blake M. Hauser
Soo Hyun Kim
Joost Brinks
Seung Hoan Choi
Yuyang Luo
FinnGen
VA Million Veteran Program
Saiju Pyarajan
Cari L. Nealon
Michael B. Gorin
Wen-Chih Wu
Scott A. Anthony
David P. Roncone
Lucia Sobrin
Kai Kaarniranta
Suzanne Yzer
Aarno Palotie
Neal S. Peachey
Joni A. Turunen
Camiel JF Boon
Patrick T. Ellinor
Sudha K. Iyengar
Mark J. Daly
Elizabeth J. Rossin
author_facet Joel T. Rämö
Bryan R. Gorman
Lu-Chen Weng
Sean J. Jurgens
Panisa Singhanetr
Marisa G. Tieger
Elon HC van Dijk
Christopher W. Halladay
Xin Wang
Blake M. Hauser
Soo Hyun Kim
Joost Brinks
Seung Hoan Choi
Yuyang Luo
FinnGen
VA Million Veteran Program
Saiju Pyarajan
Cari L. Nealon
Michael B. Gorin
Wen-Chih Wu
Scott A. Anthony
David P. Roncone
Lucia Sobrin
Kai Kaarniranta
Suzanne Yzer
Aarno Palotie
Neal S. Peachey
Joni A. Turunen
Camiel JF Boon
Patrick T. Ellinor
Sudha K. Iyengar
Mark J. Daly
Elizabeth J. Rossin
author_sort Joel T. Rämö
collection DOAJ
description Abstract Central serous chorioretinopathy is an eye disease characterized by fluid buildup under the central retina whose etiology is not well understood. Abnormal choroidal veins in central serous chorioretinopathy patients have been shown to have similarities with varicose veins. To identify potential mechanisms, we analyzed genotype data from 1,477 patients and 455,449 controls in FinnGen. We identified an association for a low-frequency (allele frequency = 0.5%) missense variant (rs113791087) in PTPRB, the gene encoding vascular endothelial protein tyrosine phosphatase (odds ratio=2.85, P = 4.5 × 10-9). This was confirmed in a meta-analysis of 2,452 patients and 865,767 controls from 4 studies (odds ratio=3.06, P = 7.4 × 10-15). Rs113791087 was associated with a 56% higher prevalence of retinal abnormalities (35.3% vs 22.6%, P = 8.0 × 10-4) in 708 UK Biobank participants and, surprisingly, with increased risk of varicose veins (odds ratio=1.31, P = 2.3 × 10-11) and reduced risk of glaucoma (odds ratio=0.82, P = 6.9 × 10-9). Predicted loss-of-function variants in PTPRB, though rare in number, were associated with central serous chorioretinopathy in All of Us (odds ratio=17.09, P = 0.018). These findings highlight the significance of vascular endothelial protein tyrosine phosphatase in diverse ocular and systemic veno-vascular diseases.
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spelling doaj-art-e5a866fcde8c4fd0b8a917aef0f72ace2025-08-20T01:47:29ZengNature PortfolioNature Communications2041-17232025-05-0116111310.1038/s41467-025-58686-6Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucomaJoel T. Rämö0Bryan R. Gorman1Lu-Chen Weng2Sean J. Jurgens3Panisa Singhanetr4Marisa G. Tieger5Elon HC van Dijk6Christopher W. Halladay7Xin Wang8Blake M. Hauser9Soo Hyun Kim10Joost Brinks11Seung Hoan Choi12Yuyang Luo13FinnGenVA Million Veteran ProgramSaiju Pyarajan14Cari L. Nealon15Michael B. Gorin16Wen-Chih Wu17Scott A. Anthony18David P. Roncone19Lucia Sobrin20Kai Kaarniranta21Suzanne Yzer22Aarno Palotie23Neal S. Peachey24Joni A. Turunen25Camiel JF Boon26Patrick T. Ellinor27Sudha K. Iyengar28Mark J. Daly29Elizabeth J. Rossin30Institute for Molecular Medicine Finland (FIMM), Helsinki Institute of Life Science (HiLIFE), University of HelsinkiCenter for Data and Computational Sciences (C-DACS), VA Cooperative Studies Program, VA Boston Healthcare SystemCardiovascular Disease Initiative, Broad Institute of MIT and HarvardCardiovascular Disease Initiative, Broad Institute of MIT and HarvardMassachusetts Eye and EarNew England Eye Center, Tufts Medical CenterDepartment of Ophthalmology, Leiden University Medical CenterCenter of Innovation in Long Term Services and Supports, Providence VA Medical CenterCardiovascular Disease Initiative, Broad Institute of MIT and HarvardMassachusetts Eye and EarMassachusetts Eye and EarDepartment of Ophthalmology, Leiden University Medical CenterDepartment of Biostatistics, Boston UniversityMassachusetts Eye and EarVA Cooperative Studies Program, VA Boston Healthcare SystemEye Clinic, VA Northeast Ohio Healthcare SystemDepartment of Ophthalmology, David Geffen School of Medicine, Stein Eye Institute, University of California, Los AngelesSection of Cardiology, Medical Service, VA Providence Healthcare SystemEye Clinic, VA Northeast Ohio Healthcare SystemEye Clinic, VA Northeast Ohio Healthcare SystemHarvard Medical School Department of Ophthalmology, Massachusetts Eye and EarDepartment of Ophthalmology, University of Eastern Finland and Kuopio University HospitalDepartment of Ophthalmology, Radboud University Medical CenterInstitute for Molecular Medicine Finland (FIMM), Helsinki Institute of Life Science (HiLIFE), University of HelsinkiResearch Service, VA Northeast Ohio Healthcare SystemFolkhälsan Research Center, BiomedicumDepartment of Ophthalmology, Leiden University Medical CenterCardiovascular Disease Initiative, Broad Institute of MIT and HarvardResearch Service, VA Northeast Ohio Healthcare SystemInstitute for Molecular Medicine Finland (FIMM), Helsinki Institute of Life Science (HiLIFE), University of HelsinkiHarvard Medical School Department of Ophthalmology, Massachusetts Eye and EarAbstract Central serous chorioretinopathy is an eye disease characterized by fluid buildup under the central retina whose etiology is not well understood. Abnormal choroidal veins in central serous chorioretinopathy patients have been shown to have similarities with varicose veins. To identify potential mechanisms, we analyzed genotype data from 1,477 patients and 455,449 controls in FinnGen. We identified an association for a low-frequency (allele frequency = 0.5%) missense variant (rs113791087) in PTPRB, the gene encoding vascular endothelial protein tyrosine phosphatase (odds ratio=2.85, P = 4.5 × 10-9). This was confirmed in a meta-analysis of 2,452 patients and 865,767 controls from 4 studies (odds ratio=3.06, P = 7.4 × 10-15). Rs113791087 was associated with a 56% higher prevalence of retinal abnormalities (35.3% vs 22.6%, P = 8.0 × 10-4) in 708 UK Biobank participants and, surprisingly, with increased risk of varicose veins (odds ratio=1.31, P = 2.3 × 10-11) and reduced risk of glaucoma (odds ratio=0.82, P = 6.9 × 10-9). Predicted loss-of-function variants in PTPRB, though rare in number, were associated with central serous chorioretinopathy in All of Us (odds ratio=17.09, P = 0.018). These findings highlight the significance of vascular endothelial protein tyrosine phosphatase in diverse ocular and systemic veno-vascular diseases.https://doi.org/10.1038/s41467-025-58686-6
spellingShingle Joel T. Rämö
Bryan R. Gorman
Lu-Chen Weng
Sean J. Jurgens
Panisa Singhanetr
Marisa G. Tieger
Elon HC van Dijk
Christopher W. Halladay
Xin Wang
Blake M. Hauser
Soo Hyun Kim
Joost Brinks
Seung Hoan Choi
Yuyang Luo
FinnGen
VA Million Veteran Program
Saiju Pyarajan
Cari L. Nealon
Michael B. Gorin
Wen-Chih Wu
Scott A. Anthony
David P. Roncone
Lucia Sobrin
Kai Kaarniranta
Suzanne Yzer
Aarno Palotie
Neal S. Peachey
Joni A. Turunen
Camiel JF Boon
Patrick T. Ellinor
Sudha K. Iyengar
Mark J. Daly
Elizabeth J. Rossin
Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma
Nature Communications
title Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma
title_full Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma
title_fullStr Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma
title_full_unstemmed Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma
title_short Rare genetic variation in PTPRB is associated with central serous chorioretinopathy, varicose veins and glaucoma
title_sort rare genetic variation in ptprb is associated with central serous chorioretinopathy varicose veins and glaucoma
url https://doi.org/10.1038/s41467-025-58686-6
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