Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report

Alagille syndrome is a rare genetic disorder causing multisystem complications, including biliary abnormalities, chronic liver disease, and rarely, hepatocellular carcinoma (HCC), which is difficult to manage due to liver dysfunction and vascular abnormalities. We report a 29-year-old female, diagno...

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Main Authors: Imad Akasbi, MD, Ismail Chaouche, MD, Nizar El Bouardi, MD, Amal Akammar, MD, Hajar O Chahdi, MD, Ismail Zerrari, MD, Maria Lahlali, MD, Hakima Abid, MD, Badr Alami, MD, Nada Lahmidani, MD, Meryem Boubbou, MD, Ibrahimi Sidi adil, MD, Mustapha Maaroufi, MD, MY Youssef Alaoui Lamrani, MD
Format: Article
Language:English
Published: Elsevier 2025-08-01
Series:Radiology Case Reports
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Online Access:http://www.sciencedirect.com/science/article/pii/S1930043325004236
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author Imad Akasbi, MD
Ismail Chaouche, MD
Nizar El Bouardi, MD
Amal Akammar, MD
Hajar O Chahdi, MD
Ismail Zerrari, MD
Maria Lahlali, MD
Hakima Abid, MD
Badr Alami, MD
Nada Lahmidani, MD
Meryem Boubbou, MD
Ibrahimi Sidi adil, MD
Mustapha Maaroufi, MD
MY Youssef Alaoui Lamrani, MD
author_facet Imad Akasbi, MD
Ismail Chaouche, MD
Nizar El Bouardi, MD
Amal Akammar, MD
Hajar O Chahdi, MD
Ismail Zerrari, MD
Maria Lahlali, MD
Hakima Abid, MD
Badr Alami, MD
Nada Lahmidani, MD
Meryem Boubbou, MD
Ibrahimi Sidi adil, MD
Mustapha Maaroufi, MD
MY Youssef Alaoui Lamrani, MD
author_sort Imad Akasbi, MD
collection DOAJ
description Alagille syndrome is a rare genetic disorder causing multisystem complications, including biliary abnormalities, chronic liver disease, and rarely, hepatocellular carcinoma (HCC), which is difficult to manage due to liver dysfunction and vascular abnormalities. We report a 29-year-old female, diagnosed with Alagille syndrome in infancy, who developed infiltrative HCC at age 20 and underwent lipiodol-based transarterial chemoembolization (TACE) in 2015, with a second session in 2016 for recurrence. Remarkably, she has achieved an exceptional 9-year survival post-treatment with stable imaging and no recurrence, a highly uncommon outcome for HCC in Alagille syndrome, highlighting TACE’s potential as an effective palliative treatment for HCC in Alagille syndrome, particularly for patient's ineligible for liver transplantation, and underscoring the need for further studies on locoregional therapies in this rare population.
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issn 1930-0433
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publishDate 2025-08-01
publisher Elsevier
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series Radiology Case Reports
spelling doaj-art-e318328df08b4793a8be6904785ed22a2025-08-20T02:30:55ZengElsevierRadiology Case Reports1930-04332025-08-012083879388510.1016/j.radcr.2025.04.125Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case reportImad Akasbi, MD0Ismail Chaouche, MD1Nizar El Bouardi, MD2Amal Akammar, MD3Hajar O Chahdi, MD4Ismail Zerrari, MD5Maria Lahlali, MD6Hakima Abid, MD7Badr Alami, MD8Nada Lahmidani, MD9Meryem Boubbou, MD10Ibrahimi Sidi adil, MD11Mustapha Maaroufi, MD12MY Youssef Alaoui Lamrani, MD13Adult Radiology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, Morocco; Corresponding author.Adult Radiology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoAdult Radiology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoRadiology Department, Mother and Child Hospital, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoRadiology Department, Mother and Child Hospital, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoGastroenterology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoGastroenterology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoGastroenterology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoAdult Radiology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, Morocco; Department of Radiology and Clinical Imaging, The Clinical Neurosciences Laboratory, Faculty of medicine and Pharmacy, University of Fez, Fez, Morocco; Department of Biophysics and Clinical MRI Methods, Faculty of Medicine and Pharmacy, University of Fez, Fez, MoroccoGastroenterology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoRadiology Department, Mother and Child Hospital, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoGastroenterology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoAdult Radiology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoAdult Radiology Department, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, Morocco; Digestive Research Laboratory, CHU Hassan II, Sidi Mohammed Ben Abdellah University, Fez, MoroccoAlagille syndrome is a rare genetic disorder causing multisystem complications, including biliary abnormalities, chronic liver disease, and rarely, hepatocellular carcinoma (HCC), which is difficult to manage due to liver dysfunction and vascular abnormalities. We report a 29-year-old female, diagnosed with Alagille syndrome in infancy, who developed infiltrative HCC at age 20 and underwent lipiodol-based transarterial chemoembolization (TACE) in 2015, with a second session in 2016 for recurrence. Remarkably, she has achieved an exceptional 9-year survival post-treatment with stable imaging and no recurrence, a highly uncommon outcome for HCC in Alagille syndrome, highlighting TACE’s potential as an effective palliative treatment for HCC in Alagille syndrome, particularly for patient's ineligible for liver transplantation, and underscoring the need for further studies on locoregional therapies in this rare population.http://www.sciencedirect.com/science/article/pii/S1930043325004236HCCLipiodol chemoembolizationAlagille syndrome
spellingShingle Imad Akasbi, MD
Ismail Chaouche, MD
Nizar El Bouardi, MD
Amal Akammar, MD
Hajar O Chahdi, MD
Ismail Zerrari, MD
Maria Lahlali, MD
Hakima Abid, MD
Badr Alami, MD
Nada Lahmidani, MD
Meryem Boubbou, MD
Ibrahimi Sidi adil, MD
Mustapha Maaroufi, MD
MY Youssef Alaoui Lamrani, MD
Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report
Radiology Case Reports
HCC
Lipiodol chemoembolization
Alagille syndrome
title Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report
title_full Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report
title_fullStr Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report
title_full_unstemmed Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report
title_short Successful long-term survival following lipiodol chemoembolization for hepatocellular carcinoma in Alagille syndrome: A case report
title_sort successful long term survival following lipiodol chemoembolization for hepatocellular carcinoma in alagille syndrome a case report
topic HCC
Lipiodol chemoembolization
Alagille syndrome
url http://www.sciencedirect.com/science/article/pii/S1930043325004236
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