Alpha-1-Antitrypsin Deficiency in Children: Case Series

Alpha-1-antitrypsin deficiency (A1AT) is a cause of an orphan disease, cases of which are well described in adult patients, but as for children, they are described only in a few publications, and in most of them the description is limited to liver lesions. This article presents the results from the...

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Main Authors: Svetlana I. Melnik, Nikolay N. Vlasov, Marina V. Pinevskaya, Elena A. Orlova, Svetlana V. Starevskaya, Irina Y. Melnikova
Format: Article
Language:English
Published: "Paediatrician" Publishers LLC 2016-12-01
Series:Вопросы современной педиатрии
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Online Access:https://vsp.spr-journal.ru/jour/article/view/1701
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author Svetlana I. Melnik
Nikolay N. Vlasov
Marina V. Pinevskaya
Elena A. Orlova
Svetlana V. Starevskaya
Irina Y. Melnikova
author_facet Svetlana I. Melnik
Nikolay N. Vlasov
Marina V. Pinevskaya
Elena A. Orlova
Svetlana V. Starevskaya
Irina Y. Melnikova
author_sort Svetlana I. Melnik
collection DOAJ
description Alpha-1-antitrypsin deficiency (A1AT) is a cause of an orphan disease, cases of which are well described in adult patients, but as for children, they are described only in a few publications, and in most of them the description is limited to liver lesions. This article presents the results from the observation of 5 children with alpha-1-antitrypsin deficiency, including 3 boys (Z-allele homozygotes) and 2 girls (PiMZ-phenotype carriers). It is shown that in patients with A1AT deficiency the onset of the destruction of lung tissue was at the age of 2 with the signs of recurrent bronchial obstruction and at the age of 7 in the form of emphysema. Raising awareness among practicing physicians of various specialties will improve diagnostics of this form of disease and its comorbid conditions.
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publisher "Paediatrician" Publishers LLC
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series Вопросы современной педиатрии
spelling doaj-art-e0e6a92e8e62411f927dcbfa0dcaaf9c2025-08-20T03:21:58Zeng"Paediatrician" Publishers LLCВопросы современной педиатрии1682-55271682-55352016-12-0115661962410.15690/vsp.v15i6.16601650Alpha-1-Antitrypsin Deficiency in Children: Case SeriesSvetlana I. Melnik0Nikolay N. Vlasov1Marina V. Pinevskaya2Elena A. Orlova3Svetlana V. Starevskaya4Irina Y. Melnikova5I.I. Mechnikov North-Western State Medical University Rauhfus Children's City Hospital No. 19, SaintSaint-Petersburg State Pediatric Medical UniversityRauhfus Children's City Hospital No. 19, SaintI.I. Mechnikov North-Western State Medical University Rauhfus Children's City Hospital No. 19, SaintI.I. Mechnikov North-Western State Medical University Rauhfus Children's City Hospital No. 19, SaintI.I. Mechnikov North-Western State Medical UniversityAlpha-1-antitrypsin deficiency (A1AT) is a cause of an orphan disease, cases of which are well described in adult patients, but as for children, they are described only in a few publications, and in most of them the description is limited to liver lesions. This article presents the results from the observation of 5 children with alpha-1-antitrypsin deficiency, including 3 boys (Z-allele homozygotes) and 2 girls (PiMZ-phenotype carriers). It is shown that in patients with A1AT deficiency the onset of the destruction of lung tissue was at the age of 2 with the signs of recurrent bronchial obstruction and at the age of 7 in the form of emphysema. Raising awareness among practicing physicians of various specialties will improve diagnostics of this form of disease and its comorbid conditions.https://vsp.spr-journal.ru/jour/article/view/1701childrenalpha-1 antitrypsin deficiencyemphysemacirrhosis
spellingShingle Svetlana I. Melnik
Nikolay N. Vlasov
Marina V. Pinevskaya
Elena A. Orlova
Svetlana V. Starevskaya
Irina Y. Melnikova
Alpha-1-Antitrypsin Deficiency in Children: Case Series
Вопросы современной педиатрии
children
alpha-1 antitrypsin deficiency
emphysema
cirrhosis
title Alpha-1-Antitrypsin Deficiency in Children: Case Series
title_full Alpha-1-Antitrypsin Deficiency in Children: Case Series
title_fullStr Alpha-1-Antitrypsin Deficiency in Children: Case Series
title_full_unstemmed Alpha-1-Antitrypsin Deficiency in Children: Case Series
title_short Alpha-1-Antitrypsin Deficiency in Children: Case Series
title_sort alpha 1 antitrypsin deficiency in children case series
topic children
alpha-1 antitrypsin deficiency
emphysema
cirrhosis
url https://vsp.spr-journal.ru/jour/article/view/1701
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AT marinavpinevskaya alpha1antitrypsindeficiencyinchildrencaseseries
AT elenaaorlova alpha1antitrypsindeficiencyinchildrencaseseries
AT svetlanavstarevskaya alpha1antitrypsindeficiencyinchildrencaseseries
AT irinaymelnikova alpha1antitrypsindeficiencyinchildrencaseseries