Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.

The molecular mechanism of human anal squamous cell carcinoma (ASCC) is unclear, and the accumulating evidence indicate association of ASCC with the activation of the Akt/mTOR pathway. Here we describe a mouse model with spontaneous anal squamous cell cancer, wherein a combined deletion of Tgfbr1 an...

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Main Authors: Zhi-Jun Sun, Lu Zhang, Wei Zhang, Bradford Hall, Yansong Bian, Ashok B Kulkarni
Format: Article
Language:English
Published: Public Library of Science (PLoS) 2013-01-01
Series:PLoS ONE
Online Access:https://doi.org/10.1371/journal.pone.0074888
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author Zhi-Jun Sun
Lu Zhang
Wei Zhang
Bradford Hall
Yansong Bian
Ashok B Kulkarni
author_facet Zhi-Jun Sun
Lu Zhang
Wei Zhang
Bradford Hall
Yansong Bian
Ashok B Kulkarni
author_sort Zhi-Jun Sun
collection DOAJ
description The molecular mechanism of human anal squamous cell carcinoma (ASCC) is unclear, and the accumulating evidence indicate association of ASCC with the activation of the Akt/mTOR pathway. Here we describe a mouse model with spontaneous anal squamous cell cancer, wherein a combined deletion of Tgfbr1 and Pten in stratified squamous epithelia was induced using inducible K14-Cre. Histopathologic analyses confirmed that 33.3% of the mice showed increased susceptibility to ASCC and precancerous lesions. Biomarker analyses demonstrated that the activation of the Akt pathway in ASCC of the Tgfbr1 and Pten double knockout (2cKO) mouse was similar to that observed in human anal cancer. Chemopreventive experiments using mTOR inhibitor-rapamycin treatment significantly delayed the onset of the ASCC tumors and reduced the tumor burden in 2cKO mice by decreasing the phosphorylation of Akt and S6. This is the first conditional knockout mouse model used for investigating the contributions of viral and cellular factors in anal carcinogenesis without carcinogen-mediated induction, and it would provide a platform for assessing new therapeutic modalities for treating and/or preventing this type of cancer.
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spelling doaj-art-deca029d370b431a9e6002e2fe98f9742025-08-20T03:10:42ZengPublic Library of Science (PLoS)PLoS ONE1932-62032013-01-01810e7488810.1371/journal.pone.0074888Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.Zhi-Jun SunLu ZhangWei ZhangBradford HallYansong BianAshok B KulkarniThe molecular mechanism of human anal squamous cell carcinoma (ASCC) is unclear, and the accumulating evidence indicate association of ASCC with the activation of the Akt/mTOR pathway. Here we describe a mouse model with spontaneous anal squamous cell cancer, wherein a combined deletion of Tgfbr1 and Pten in stratified squamous epithelia was induced using inducible K14-Cre. Histopathologic analyses confirmed that 33.3% of the mice showed increased susceptibility to ASCC and precancerous lesions. Biomarker analyses demonstrated that the activation of the Akt pathway in ASCC of the Tgfbr1 and Pten double knockout (2cKO) mouse was similar to that observed in human anal cancer. Chemopreventive experiments using mTOR inhibitor-rapamycin treatment significantly delayed the onset of the ASCC tumors and reduced the tumor burden in 2cKO mice by decreasing the phosphorylation of Akt and S6. This is the first conditional knockout mouse model used for investigating the contributions of viral and cellular factors in anal carcinogenesis without carcinogen-mediated induction, and it would provide a platform for assessing new therapeutic modalities for treating and/or preventing this type of cancer.https://doi.org/10.1371/journal.pone.0074888
spellingShingle Zhi-Jun Sun
Lu Zhang
Wei Zhang
Bradford Hall
Yansong Bian
Ashok B Kulkarni
Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.
PLoS ONE
title Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.
title_full Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.
title_fullStr Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.
title_full_unstemmed Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.
title_short Inhibition of mTOR reduces anal carcinogenesis in transgenic mouse model.
title_sort inhibition of mtor reduces anal carcinogenesis in transgenic mouse model
url https://doi.org/10.1371/journal.pone.0074888
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AT yansongbian inhibitionofmtorreducesanalcarcinogenesisintransgenicmousemodel
AT ashokbkulkarni inhibitionofmtorreducesanalcarcinogenesisintransgenicmousemodel