Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies

Abstract Mitochondrial defects can lead to cardiomyopathies, which can be particularly severe in children. However, many cases of pediatric cardiomyopathy have no known etiology. To address this, we sought to explore if mitochondrial genome defects might be a contributor, as this could offer insight...

Full description

Saved in:
Bibliographic Details
Main Authors: M. Arda Temena, Ebru Erzurumluoglu Gokalp, Ezgi Susam, Duygu Cinar, Hikmet Kiztanir, Pelin Kosger, Beyhan Durak Aras, Sevilhan Artan, Oguz Cilingir
Format: Article
Language:English
Published: Nature Portfolio 2025-05-01
Series:Scientific Reports
Online Access:https://doi.org/10.1038/s41598-025-01007-0
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849744645364383744
author M. Arda Temena
Ebru Erzurumluoglu Gokalp
Ezgi Susam
Duygu Cinar
Hikmet Kiztanir
Pelin Kosger
Beyhan Durak Aras
Sevilhan Artan
Oguz Cilingir
author_facet M. Arda Temena
Ebru Erzurumluoglu Gokalp
Ezgi Susam
Duygu Cinar
Hikmet Kiztanir
Pelin Kosger
Beyhan Durak Aras
Sevilhan Artan
Oguz Cilingir
author_sort M. Arda Temena
collection DOAJ
description Abstract Mitochondrial defects can lead to cardiomyopathies, which can be particularly severe in children. However, many cases of pediatric cardiomyopathy have no known etiology. To address this, we sought to explore if mitochondrial genome defects might be a contributor, as this could offer insights into disease mechanisms and guide targeted interventions. We first sequenced cardiomyopathy-related genes in twenty-seven pediatric patients diagnosed with primary non-syndromic cardiomyopathy and performed whole mtDNA sequencing in both patients and thirty-one healthy controls. The initial sequencing identified pathogenic variants in seven patients but subsequent mtDNA sequencing revealed additional insights. Specifically, a variant in FOXRED1, encoding FAD-dependent oxidoreductase domain-containing protein-1 which functions in mitochondrial complex I stability, and another variant in cytochrome c oxidase-I, MT-CO1, crucial for aerobic metabolism, were identified in two siblings with hypertrophic cardiomyopathy. In another case with hypertrophic cardiomyopathy, a variant in cytochrome b, MT-CYB, is likely a key factor in the abnormal contraction of cardiac muscle contraction. Furthermore, a novel 12 S rRNA variant was found in a patient with left ventricular non-compaction, and this offers a promising explanation for the pathogenesis, given the gene’s high expression in the left ventricle. Taken together, mtDNA variants act synergistically with others, potentially disrupting myocardial bioenergetics.
format Article
id doaj-art-db4be541354a4d4782a46cdcb0e94a2c
institution DOAJ
issn 2045-2322
language English
publishDate 2025-05-01
publisher Nature Portfolio
record_format Article
series Scientific Reports
spelling doaj-art-db4be541354a4d4782a46cdcb0e94a2c2025-08-20T03:10:13ZengNature PortfolioScientific Reports2045-23222025-05-0115111410.1038/s41598-025-01007-0Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathiesM. Arda Temena0Ebru Erzurumluoglu Gokalp1Ezgi Susam2Duygu Cinar3Hikmet Kiztanir4Pelin Kosger5Beyhan Durak Aras6Sevilhan Artan7Oguz Cilingir8Science & Technology Policy Studies, METUMedical Genetics Department, Eskişehir Osmangazi UniversityMedical Genetics Department, Eskişehir Osmangazi UniversityMedical Genetics Department, Eskişehir Osmangazi UniversityChild Health and Diseases Department, Eskişehir Osmangazi UniversityChild Health and Diseases Department, Eskişehir Osmangazi UniversityMedical Genetics Department, Eskişehir Osmangazi UniversityMedical Genetics Department, Eskişehir Osmangazi UniversityMedical Genetics Department, Eskişehir Osmangazi UniversityAbstract Mitochondrial defects can lead to cardiomyopathies, which can be particularly severe in children. However, many cases of pediatric cardiomyopathy have no known etiology. To address this, we sought to explore if mitochondrial genome defects might be a contributor, as this could offer insights into disease mechanisms and guide targeted interventions. We first sequenced cardiomyopathy-related genes in twenty-seven pediatric patients diagnosed with primary non-syndromic cardiomyopathy and performed whole mtDNA sequencing in both patients and thirty-one healthy controls. The initial sequencing identified pathogenic variants in seven patients but subsequent mtDNA sequencing revealed additional insights. Specifically, a variant in FOXRED1, encoding FAD-dependent oxidoreductase domain-containing protein-1 which functions in mitochondrial complex I stability, and another variant in cytochrome c oxidase-I, MT-CO1, crucial for aerobic metabolism, were identified in two siblings with hypertrophic cardiomyopathy. In another case with hypertrophic cardiomyopathy, a variant in cytochrome b, MT-CYB, is likely a key factor in the abnormal contraction of cardiac muscle contraction. Furthermore, a novel 12 S rRNA variant was found in a patient with left ventricular non-compaction, and this offers a promising explanation for the pathogenesis, given the gene’s high expression in the left ventricle. Taken together, mtDNA variants act synergistically with others, potentially disrupting myocardial bioenergetics.https://doi.org/10.1038/s41598-025-01007-0
spellingShingle M. Arda Temena
Ebru Erzurumluoglu Gokalp
Ezgi Susam
Duygu Cinar
Hikmet Kiztanir
Pelin Kosger
Beyhan Durak Aras
Sevilhan Artan
Oguz Cilingir
Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
Scientific Reports
title Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
title_full Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
title_fullStr Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
title_full_unstemmed Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
title_short Investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
title_sort investigating the dual role of mitochondrial and nuclear genome variants in pediatric cardiomyopathies
url https://doi.org/10.1038/s41598-025-01007-0
work_keys_str_mv AT mardatemena investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT ebruerzurumluoglugokalp investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT ezgisusam investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT duygucinar investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT hikmetkiztanir investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT pelinkosger investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT beyhandurakaras investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT sevilhanartan investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies
AT oguzcilingir investigatingthedualroleofmitochondrialandnucleargenomevariantsinpediatriccardiomyopathies