Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study

Background. Tenapanor is a locally acting selective sodium-hydrogen exchanger 3 inhibitor with the potential to treat sodium/phosphorus and fluid overload in various cardiac-renal diseases, which has been approved for constipation-predominant irritable bowel syndrome in the US. The pharmacokinetics...

Full description

Saved in:
Bibliographic Details
Main Authors: Gang Yuan, Yili Chen, Li Li, Xin Wang, Gang Wei, Jiawei Zeng, Ai-Min Hui, Yueyun Jiang, Han Zhao, Lei Diao, Yongchun Zhou, Yinglian Xiao, Minhu Chen
Format: Article
Language:English
Published: Wiley 2024-01-01
Series:International Journal of Clinical Practice
Online Access:http://dx.doi.org/10.1155/2024/1386980
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1849473172981678080
author Gang Yuan
Yili Chen
Li Li
Xin Wang
Gang Wei
Jiawei Zeng
Ai-Min Hui
Yueyun Jiang
Han Zhao
Lei Diao
Yongchun Zhou
Yinglian Xiao
Minhu Chen
author_facet Gang Yuan
Yili Chen
Li Li
Xin Wang
Gang Wei
Jiawei Zeng
Ai-Min Hui
Yueyun Jiang
Han Zhao
Lei Diao
Yongchun Zhou
Yinglian Xiao
Minhu Chen
author_sort Gang Yuan
collection DOAJ
description Background. Tenapanor is a locally acting selective sodium-hydrogen exchanger 3 inhibitor with the potential to treat sodium/phosphorus and fluid overload in various cardiac-renal diseases, which has been approved for constipation-predominant irritable bowel syndrome in the US. The pharmacokinetics (PK) of tenapanor and its metabolite tenapanor-M1 (AZ13792925), as well as the safety and tolerability of tenapanor, were investigated in healthy Chinese and Caucasian subjects. Methods. This randomized, open-label, single-center, placebo-controlled phase 1 study (https://www.chinadrugtrials.org.cn; CTR20201783) enrolled Chinese and Caucasian healthy volunteers into 4 parallel cohorts (3 cohorts for Chinese subjects, 1 cohort for Caucasian subjects). In each cohort, 15 subjects were expected to be included and received oral tenapanor (10 or 30 mg as single dose, or 50 mg as a single dose followed by a twice-daily repeated dose from Day 5 to 11, with a single dose in the morning on Day 11) or placebo in a 4 : 1 ratio. Results. 59 healthy volunteers received tenapanor 10 mg (n = 12 Chinese), 30 mg (n = 12 Chinese), or 50 mg (n = 12 (Chinese), n = 11 (Caucasian)) or placebo (n = 12, 3 per cohort). After single and twice-daily repeated doses, tenapanor plasma concentrations were all below the limit of quantitation; tenapanor-M1 appeared slowly in plasma. In single-ascending dose evaluation (10 to 50 mg) of Chinese subjects, the mean Cmax, AUC0-t, and AUC0-∞ of tenapanor-M1 increased with increasing dose level, and AUC0-t increased approximately dose proportionally. The Cmax accumulation ratio was 1.55 to 6.92 after 50 mg repeated dose in Chinese and Caucasian subjects. Exposure to tenapanor-M1 was generally similar between the Chinese and Caucasian subjects. Tenapanor was generally well-tolerated and the safety profile was similar between the Chinese and Caucasian participants receiving tenapanor 50 mg, as measured by vital signs, physical and laboratory examination, 12-lead ECG, and adverse events. No serious adverse event or adverse event leading to withdrawal occurred. Conclusion. Tenapanor was well-tolerated, with similar PK and safety profiles between Chinese and Caucasian subjects. This trial is registered with CTR20201783.
format Article
id doaj-art-d85dbf56ed6043709878e54acef2fe34
institution Kabale University
issn 1742-1241
language English
publishDate 2024-01-01
publisher Wiley
record_format Article
series International Journal of Clinical Practice
spelling doaj-art-d85dbf56ed6043709878e54acef2fe342025-08-20T03:24:15ZengWileyInternational Journal of Clinical Practice1742-12412024-01-01202410.1155/2024/1386980Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 StudyGang Yuan0Yili Chen1Li Li2Xin Wang3Gang Wei4Jiawei Zeng5Ai-Min Hui6Yueyun Jiang7Han Zhao8Lei Diao9Yongchun Zhou10Yinglian Xiao11Minhu Chen12The First Affiliated HospitalThe First Affiliated HospitalThe First Affiliated HospitalGlobal R&D CenterGlobal R&D CenterThe First Affiliated HospitalGlobal R&D CenterThe First Affiliated HospitalGlobal R&D CenterGlobal R&D CenterWanbang BiopharmaceuticalsThe First Affiliated HospitalThe First Affiliated HospitalBackground. Tenapanor is a locally acting selective sodium-hydrogen exchanger 3 inhibitor with the potential to treat sodium/phosphorus and fluid overload in various cardiac-renal diseases, which has been approved for constipation-predominant irritable bowel syndrome in the US. The pharmacokinetics (PK) of tenapanor and its metabolite tenapanor-M1 (AZ13792925), as well as the safety and tolerability of tenapanor, were investigated in healthy Chinese and Caucasian subjects. Methods. This randomized, open-label, single-center, placebo-controlled phase 1 study (https://www.chinadrugtrials.org.cn; CTR20201783) enrolled Chinese and Caucasian healthy volunteers into 4 parallel cohorts (3 cohorts for Chinese subjects, 1 cohort for Caucasian subjects). In each cohort, 15 subjects were expected to be included and received oral tenapanor (10 or 30 mg as single dose, or 50 mg as a single dose followed by a twice-daily repeated dose from Day 5 to 11, with a single dose in the morning on Day 11) or placebo in a 4 : 1 ratio. Results. 59 healthy volunteers received tenapanor 10 mg (n = 12 Chinese), 30 mg (n = 12 Chinese), or 50 mg (n = 12 (Chinese), n = 11 (Caucasian)) or placebo (n = 12, 3 per cohort). After single and twice-daily repeated doses, tenapanor plasma concentrations were all below the limit of quantitation; tenapanor-M1 appeared slowly in plasma. In single-ascending dose evaluation (10 to 50 mg) of Chinese subjects, the mean Cmax, AUC0-t, and AUC0-∞ of tenapanor-M1 increased with increasing dose level, and AUC0-t increased approximately dose proportionally. The Cmax accumulation ratio was 1.55 to 6.92 after 50 mg repeated dose in Chinese and Caucasian subjects. Exposure to tenapanor-M1 was generally similar between the Chinese and Caucasian subjects. Tenapanor was generally well-tolerated and the safety profile was similar between the Chinese and Caucasian participants receiving tenapanor 50 mg, as measured by vital signs, physical and laboratory examination, 12-lead ECG, and adverse events. No serious adverse event or adverse event leading to withdrawal occurred. Conclusion. Tenapanor was well-tolerated, with similar PK and safety profiles between Chinese and Caucasian subjects. This trial is registered with CTR20201783.http://dx.doi.org/10.1155/2024/1386980
spellingShingle Gang Yuan
Yili Chen
Li Li
Xin Wang
Gang Wei
Jiawei Zeng
Ai-Min Hui
Yueyun Jiang
Han Zhao
Lei Diao
Yongchun Zhou
Yinglian Xiao
Minhu Chen
Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study
International Journal of Clinical Practice
title Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study
title_full Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study
title_fullStr Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study
title_full_unstemmed Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study
title_short Pharmacokinetics, Safety, and Tolerability of Tenapanor in Healthy Chinese and Caucasian Volunteers: A Randomized, Open-Label, Single-Center, Placebo-Controlled Phase 1 Study
title_sort pharmacokinetics safety and tolerability of tenapanor in healthy chinese and caucasian volunteers a randomized open label single center placebo controlled phase 1 study
url http://dx.doi.org/10.1155/2024/1386980
work_keys_str_mv AT gangyuan pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT yilichen pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT lili pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT xinwang pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT gangwei pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT jiaweizeng pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT aiminhui pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT yueyunjiang pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT hanzhao pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT leidiao pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT yongchunzhou pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT yinglianxiao pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study
AT minhuchen pharmacokineticssafetyandtolerabilityoftenapanorinhealthychineseandcaucasianvolunteersarandomizedopenlabelsinglecenterplacebocontrolledphase1study