Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay

Idiopathic pulmonary fibrosis (IPF) is a chronic and progressive age-related lung disease with an average survival of 3–5 years post-diagnosis if left untreated. It is characterized by lung fibrosis, inflammation, and destruction of lung architecture, leading to worsening respiratory symptoms and ph...

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Main Authors: Elisabeth Bäck, Jessica Bjärkby, Leire Escudero-Ibarz, Stefan Tångefjord, Johan Jirholt, Mei Ding
Format: Article
Language:English
Published: Elsevier 2025-04-01
Series:SLAS Discovery
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Online Access:http://www.sciencedirect.com/science/article/pii/S247255522500019X
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author Elisabeth Bäck
Jessica Bjärkby
Leire Escudero-Ibarz
Stefan Tångefjord
Johan Jirholt
Mei Ding
author_facet Elisabeth Bäck
Jessica Bjärkby
Leire Escudero-Ibarz
Stefan Tångefjord
Johan Jirholt
Mei Ding
author_sort Elisabeth Bäck
collection DOAJ
description Idiopathic pulmonary fibrosis (IPF) is a chronic and progressive age-related lung disease with an average survival of 3–5 years post-diagnosis if left untreated. It is characterized by lung fibrosis, inflammation, and destruction of lung architecture, leading to worsening respiratory symptoms and physiological impairment, ultimately culminating in progressive respiratory failure. The development of novel therapeutics for the treatment of IPF represents a significant unmet medical need. Fibroblast to myofibroblast transition (FMT) in response to fibrogenic mediators such as transforming growth factor beta 1 (TGF-β1) has been identified as a key cellular phenotype driving the formation of myofibroblasts and lung fibrosis in IPF. Establishing a robust and high-throughput in vitro human FMT assay is crucial for uncovering new disease targets and for efficiently screening compounds for the advancement of novel therapeutics aimed at targeting myofibroblast activity. However, creating a robust FMT assay suitable for high-throughput drug screening has proven challenging due to the requisite level of automation.In this study, we focus on evaluating different automation approaches for liquid exchange and compound dosing in the human FMT assay. A semi-automated assay, capable of screening a large number of compounds that inhibit TGF-β1-induced FMT in both Normal Human Lung Fibroblasts (NHLF) and IPF-patient derived Disease Human Lung Fibroblasts (IPF-DHLF), has been successfully developed and optimized. We demonstrate that the optimized FMT assay using liquid handling automation exhibits great assay reproducibility, shows good assay translation using human lung fibroblasts from normal healthy versus IPF-patients, and demonstrates acceptable human primary donor variability. This allows for the standardization of comparisons of compound anti-fibrotic potency across IPF projects.
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spelling doaj-art-d738650d40fe4aa09b0c20f2d37123332025-08-20T02:18:35ZengElsevierSLAS Discovery2472-55522025-04-013210022610.1016/j.slasd.2025.100226Enhancing throughput and robustness of the fibroblast to myofibroblast transition assayElisabeth Bäck0Jessica Bjärkby1Leire Escudero-Ibarz2Stefan Tångefjord3Johan Jirholt4Mei Ding5Bioscience, Respiratory, Inflammation and Autoimmune, R&D, AstraZeneca, Gothenburg, SwedenBioscience, Respiratory, Inflammation and Autoimmune, R&D, AstraZeneca, Gothenburg, SwedenDiscovery Sciences, R&D, AstraZeneca, Cambridge, UKBioscience, Respiratory, Inflammation and Autoimmune, R&D, AstraZeneca, Gothenburg, SwedenBioscience, Respiratory, Inflammation and Autoimmune, R&D, AstraZeneca, Gothenburg, SwedenDiscovery Sciences, R&D, AstraZeneca, Gothenburg, Sweden; Corresponding author.Idiopathic pulmonary fibrosis (IPF) is a chronic and progressive age-related lung disease with an average survival of 3–5 years post-diagnosis if left untreated. It is characterized by lung fibrosis, inflammation, and destruction of lung architecture, leading to worsening respiratory symptoms and physiological impairment, ultimately culminating in progressive respiratory failure. The development of novel therapeutics for the treatment of IPF represents a significant unmet medical need. Fibroblast to myofibroblast transition (FMT) in response to fibrogenic mediators such as transforming growth factor beta 1 (TGF-β1) has been identified as a key cellular phenotype driving the formation of myofibroblasts and lung fibrosis in IPF. Establishing a robust and high-throughput in vitro human FMT assay is crucial for uncovering new disease targets and for efficiently screening compounds for the advancement of novel therapeutics aimed at targeting myofibroblast activity. However, creating a robust FMT assay suitable for high-throughput drug screening has proven challenging due to the requisite level of automation.In this study, we focus on evaluating different automation approaches for liquid exchange and compound dosing in the human FMT assay. A semi-automated assay, capable of screening a large number of compounds that inhibit TGF-β1-induced FMT in both Normal Human Lung Fibroblasts (NHLF) and IPF-patient derived Disease Human Lung Fibroblasts (IPF-DHLF), has been successfully developed and optimized. We demonstrate that the optimized FMT assay using liquid handling automation exhibits great assay reproducibility, shows good assay translation using human lung fibroblasts from normal healthy versus IPF-patients, and demonstrates acceptable human primary donor variability. This allows for the standardization of comparisons of compound anti-fibrotic potency across IPF projects.http://www.sciencedirect.com/science/article/pii/S247255522500019XIdiopathic pulmonary fibrosisLung fibroblastFibroblast to myofibroblast transitionConfocal imagingAutomationHigh throughput
spellingShingle Elisabeth Bäck
Jessica Bjärkby
Leire Escudero-Ibarz
Stefan Tångefjord
Johan Jirholt
Mei Ding
Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
SLAS Discovery
Idiopathic pulmonary fibrosis
Lung fibroblast
Fibroblast to myofibroblast transition
Confocal imaging
Automation
High throughput
title Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
title_full Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
title_fullStr Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
title_full_unstemmed Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
title_short Enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
title_sort enhancing throughput and robustness of the fibroblast to myofibroblast transition assay
topic Idiopathic pulmonary fibrosis
Lung fibroblast
Fibroblast to myofibroblast transition
Confocal imaging
Automation
High throughput
url http://www.sciencedirect.com/science/article/pii/S247255522500019X
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